scholarly journals Long-term outcomes of patients with mucopolysaccharidosis VI treated with galsulfase enzyme replacement therapy since infancy

2021 ◽  
Vol 133 (1) ◽  
pp. 100-108
Author(s):  
Paula Garcia ◽  
Dawn Phillips ◽  
JoAnn Johnson ◽  
Kenneth Martin ◽  
Linda M. Randolph ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Long Term Outcomes ◽  
Enzyme Replacement ◽  
Mucopolysaccharidosis Vi

scholarly journals Long-term outcomes with agalsidase alfa enzyme replacement therapy: Analysis using deconstructed composite events

2018 ◽  
Vol 14 ◽  
pp. 31-35 ◽  
Author(s):  
Michael Beck ◽  
Derralynn Hughes ◽  
Christoph Kampmann ◽  
Guillem Pintos-Morell ◽  
Uma Ramaswami ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Long Term Outcomes ◽  
Enzyme Replacement ◽  
Agalsidase Alfa ◽  
Composite Events

scholarly journals Long-term outcomes with agalsidase alfa enzyme replacement therapy: Analysis using deconstructed composite events

2016 ◽  
Vol 117 (2) ◽  
pp. S25 ◽  
Author(s):  
Michael Beck ◽  
Derralynn Hughes ◽  
Christoph Kampmann ◽  
Svetlana Bizjajeva ◽  
Guillem Pintos-Morell ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Long Term Outcomes ◽  
Enzyme Replacement ◽  
Agalsidase Alfa ◽  
Composite Events

scholarly journals Long-term galsulfase enzyme replacement therapy in Taiwanese mucopolysaccharidosis VI patients: A case series

2016 ◽  
Vol 7 ◽  
pp. 63-69 ◽  
Author(s):  
Hsiang-Yu Lin ◽  
Chih-Kuang Chuang ◽  
Chung-Hsing Wang ◽  
Yin-Hsiu Chien ◽  
Yu-Mei Wang ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Case Series ◽  
Enzyme Replacement ◽  
Mucopolysaccharidosis Vi

scholarly journals Retrospective study of long-term outcomes of enzyme replacement therapy in Fabry disease: Analysis of prognostic factors

PLoS ONE ◽  
2017 ◽  
Vol 12 (8) ◽  
pp. e0182379 ◽  
Author(s):  
Maarten Arends ◽  
Marieke Biegstraaten ◽  
Derralynn A. Hughes ◽  
Atul Mehta ◽  
Perry M. Elliott ◽  
...  
Keyword(s):  
Prognostic Factors ◽  
Retrospective Study ◽  
Enzyme Replacement Therapy ◽  
Fabry Disease ◽  
Replacement Therapy ◽  
Long Term Outcomes ◽  
Enzyme Replacement ◽  
Disease Analysis
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