scholarly journals Retrospective study of long-term outcomes of enzyme replacement therapy in Fabry disease: Analysis of prognostic factors

PLoS ONE ◽  
2017 ◽  
Vol 12 (8) ◽  
pp. e0182379 ◽  
Author(s):  
Maarten Arends ◽  
Marieke Biegstraaten ◽  
Derralynn A. Hughes ◽  
Atul Mehta ◽  
Perry M. Elliott ◽  
...  
2019 ◽  
Vol 60 (1) ◽  
pp. 208-214
Author(s):  
Miki Tsujiuchi ◽  
Mio Ebato ◽  
Hideyuki Maezawa ◽  
Takuya Mizukami ◽  
Ayaka Nogi ◽  
...  

2012 ◽  
Vol 34 (4) ◽  
pp. e22
Author(s):  
E.K. Baumgärtner ◽  
M. Niemann ◽  
A. Emmert ◽  
F. Breunig ◽  
J. Strotmann ◽  
...  

2014 ◽  
Vol 37 (6) ◽  
pp. 969-978 ◽  
Author(s):  
L. J. Anderson ◽  
K. M. Wyatt ◽  
W. Henley ◽  
V. Nikolaou ◽  
S. Waldek ◽  
...  

Nephron ◽  
2016 ◽  
Vol 134 (1) ◽  
pp. 30-36 ◽  
Author(s):  
Daniel Oder ◽  
Peter Nordbeck ◽  
Christoph Wanner

Sign in / Sign up

Export Citation Format

Share Document