Retrospective study of long-term outcomes of enzyme replacement therapy in Fabry disease: Analysis of prognostic factors
2017 ◽
Vol 12
(8)
◽
pp. e0182379
◽
Maarten Arends
◽
Marieke Biegstraaten
◽
Derralynn A. Hughes
◽
Atul Mehta
◽
Perry M. Elliott
◽
...
2019 ◽
Vol 60
(1)
◽
pp. 208-214
Miki Tsujiuchi
◽
Mio Ebato
◽
Hideyuki Maezawa
◽
Takuya Mizukami
◽
Ayaka Nogi
◽
...
2013 ◽
Vol 29
(3)
◽
pp. 619-625
◽
T. Prabakaran
◽
H. Birn
◽
B. M. Bibby
◽
A. Regeniter
◽
S. S. Sorensen
◽
...
2017 ◽
Vol 120
(1-2)
◽
pp. S33
Gustavo H Cabrera
◽
Juan Manuel Politei
2019 ◽
Vol 60
(5)
◽
pp. 577-578
◽
Hsiang-Yu Lin
◽
Chung-Lin Lee
◽
Chih-Kuang Chuang
◽
Shuan-Pei Lin
A. Boyd
◽
N. Sadick
◽
D. Silence
◽
L. Thomas
2010 ◽
Vol 64
(7)
◽
pp. 995-995
◽
I. Martin-Suárez
◽
C. Suárez-Marrero
2012 ◽
Vol 34
(4)
◽
pp. e22
E.K. Baumgärtner
◽
M. Niemann
◽
A. Emmert
◽
F. Breunig
◽
J. Strotmann
◽
...
2014 ◽
Vol 37
(6)
◽
pp. 969-978
◽
L. J. Anderson
◽
K. M. Wyatt
◽
W. Henley
◽
V. Nikolaou
◽
S. Waldek
◽
...
2016 ◽
Vol 134
(1)
◽
pp. 30-36
◽
Daniel Oder
◽
Peter Nordbeck
◽
Christoph Wanner
2011 ◽
Vol 117
(1)
◽
pp. 19-28
◽
G. Messalli
◽
M. Imbriaco
◽
G. Avitabile
◽
R. Russo
◽
D. Iodice
◽
...