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390. Non-Integrating Lentiviral Vectors for Efficient and Transient Delivery of Zinc Finger Nucleases and Donor Constructs for Site-Specific Gene Correction
Molecular Therapy
◽
10.1016/s1525-0016(16)36194-9
◽
2012
◽
Vol 20
◽
pp. S152-S153
Keyword(s):
Zinc Finger
◽
Lentiviral Vectors
◽
Zinc Finger Nucleases
◽
Specific Gene
◽
Gene Correction
◽
Site Specific
Download Full-text
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References
309. Site-Specific Gene Correction of β-Globin Using Zinc Finger Nucleases
Molecular Therapy
◽
10.1016/s1525-0016(16)36113-5
◽
2012
◽
Vol 20
◽
pp. S122
Keyword(s):
Zinc Finger
◽
Zinc Finger Nucleases
◽
Specific Gene
◽
Gene Correction
◽
Site Specific
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486. Efficient Site-Specific Integration and In Situ Gene Correction of Human Long-Term Repopulating Hematopoietic Stem Cells by Zinc Finger Nucleases
Molecular Therapy
◽
10.1016/s1525-0016(16)34821-3
◽
2013
◽
Vol 21
◽
pp. S187-S188
Keyword(s):
Stem Cells
◽
Hematopoietic Stem Cells
◽
Zinc Finger
◽
Zinc Finger Nucleases
◽
Gene Correction
◽
Hematopoietic Stem
◽
Site Specific
◽
Site Specific Integration
Download Full-text
321. Efficient Gene Correction and Targeted Gene Addition in Human Stem Cells Using Engineered Zinc Finger Nucleases and Integrase-Defective Lentiviral Vectors
Molecular Therapy
◽
10.1016/s1525-0016(16)44527-2
◽
2007
◽
Vol 15
◽
pp. S121
Keyword(s):
Stem Cells
◽
Zinc Finger
◽
Lentiviral Vectors
◽
Zinc Finger Nucleases
◽
Human Stem Cells
◽
Gene Correction
◽
Efficient Gene
Download Full-text
303. Efficient Site-Specific Integration in Human Hematopoietic Stem and Progenitor Cells by Zinc Finger Nucleases and Integrase-Defective Lentiviral Vectors
Molecular Therapy
◽
10.1016/s1525-0016(16)36107-x
◽
2012
◽
Vol 20
◽
pp. S120
Keyword(s):
Progenitor Cells
◽
Zinc Finger
◽
Lentiviral Vectors
◽
Zinc Finger Nucleases
◽
Hematopoietic Stem
◽
Site Specific
◽
Site Specific Integration
◽
Stem And Progenitor Cells
Download Full-text
11. Zinc Finger Nucleases Drive Efficient Gene Disruption and Site-Specific Gene Addition in Human HSC
Molecular Therapy
◽
10.1016/s1525-0016(16)37452-4
◽
2010
◽
Vol 18
◽
pp. S5
Keyword(s):
Zinc Finger
◽
Gene Disruption
◽
Zinc Finger Nucleases
◽
Specific Gene
◽
Site Specific
◽
Efficient Gene
Download Full-text
Faculty Opinions recommendation of Highly efficient endogenous human gene correction using designed zinc-finger nucleases.
Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature
◽
10.3410/f.1025053.327438
◽
2005
◽
Author(s):
Charles Coutelle
Keyword(s):
Zinc Finger
◽
Human Gene
◽
Zinc Finger Nucleases
◽
Gene Correction
◽
Highly Efficient
Download Full-text
Faculty Opinions recommendation of Highly efficient endogenous human gene correction using designed zinc-finger nucleases.
Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature
◽
10.3410/f.1025053.325338
◽
2005
◽
Author(s):
Daniel Reines
Keyword(s):
Zinc Finger
◽
Human Gene
◽
Zinc Finger Nucleases
◽
Gene Correction
◽
Highly Efficient
Download Full-text
Faculty Opinions recommendation of Highly efficient endogenous human gene correction using designed zinc-finger nucleases.
Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature
◽
10.3410/f.1025053.296716
◽
2005
◽
Author(s):
Barry Stoddard
Keyword(s):
Zinc Finger
◽
Human Gene
◽
Zinc Finger Nucleases
◽
Gene Correction
◽
Highly Efficient
Download Full-text
Faculty Opinions recommendation of Site-specific genome editing in Plasmodium falciparum using engineered zinc-finger nucleases.
Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature
◽
10.3410/f.717963022.793465051
◽
2012
◽
Author(s):
Frank Seeber
Keyword(s):
Plasmodium Falciparum
◽
Genome Editing
◽
Zinc Finger
◽
Zinc Finger Nucleases
◽
Site Specific
Download Full-text
709. Gene Correction and Gene Knockouts in Human Somatic Cells Using Zinc Finger Nucleases
Molecular Therapy
◽
10.1016/j.ymthe.2004.06.726
◽
2004
◽
Vol 9
◽
pp. S270
Keyword(s):
Zinc Finger
◽
Somatic Cells
◽
Zinc Finger Nucleases
◽
Gene Correction
◽
Gene Knockouts
Download Full-text
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