scholarly journals Gene Therapeutic Approach Using Mutation-adapted U1 snRNA to Correct a RPGR Splice Defect in Patient-derived Cells

2011 ◽  
Vol 19 (5) ◽  
pp. 936-941 ◽  
Author(s):  
Esther Glaus ◽  
Fabian Schmid ◽  
Romain Da Costa ◽  
Wolfgang Berger ◽  
John Neidhardt



Planta Medica ◽  
2013 ◽  
Vol 79 (13) ◽  
Author(s):  
O Kelber ◽  
J Müller ◽  
SN Okpanyi ◽  
K Nieber ◽  
C Kolb
Keyword(s):  


2010 ◽  
Vol 49 (05) ◽  
pp. N41-N43
Author(s):  
T. Winder ◽  
A. Schuster ◽  
A. Becherer ◽  
K. Gasser ◽  
A. De Vries ◽  
...  


2008 ◽  
Vol 56 (S 1) ◽  
Author(s):  
B Niemann ◽  
M Teschner ◽  
S Gruenler ◽  
RE Silber ◽  
S Rohrbach


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