Gene Therapeutic Approach Using Mutation-adapted U1 snRNA to Correct a RPGR Splice Defect in Patient-derived Cells
2011 ◽
Vol 19
(5)
◽
pp. 936-941
◽
Esther Glaus
◽
Fabian Schmid
◽
Romain Da Costa
◽
Wolfgang Berger
◽
John Neidhardt
O Kelber
◽
J Müller
◽
SN Okpanyi
◽
K Nieber
◽
C Kolb
2010 ◽
Vol 49
(05)
◽
pp. N41-N43
T. Winder
◽
A. Schuster
◽
A. Becherer
◽
K. Gasser
◽
A. De Vries
◽
...
Sabrina Borchert
◽
Pia Suckrau
◽
Michael Wessolly
◽
Jan Schmeller
◽
Elena Mairinger
◽
...
B Niemann
◽
M Teschner
◽
S Gruenler
◽
RE Silber
◽
S Rohrbach