Intrapleural Administration of a Second-Generation Oxidation Resistant Alpha 1-Antitrypsin Gene Therapy for Alpha 1-Antitrypsin Deficiency

Oxidation Resistant ◽

Alpha 1 Antitrypsin ◽

Intrapleural Administration

Gene Therapy for Alpha-1-Antitrypsin Deficiency Diseases

Gene Therapy Applications ◽

10.5772/17415 ◽

2011 ◽

Author(s):

Parveen Salahuddin

Keyword(s):

Gene Therapy ◽

Antitrypsin Deficiency ◽

Alpha 1 Antitrypsin ◽

Deficiency Diseases

DNA diagnostics and approaches to gene therapy of hereditary α1-antitrypsin deficiency

Biopolymers and Cell ◽

10.7124/bc.000247 ◽

1990 ◽

Vol 6 (1) ◽

pp. 51-56

Author(s):

A. L. Schwartzman ◽

M. P. Strakhova ◽

V. S. Gaitskhoki ◽

W. Berger ◽

Ch. Coutelle

Keyword(s):

Gene Therapy ◽

Dna Diagnostics ◽

Antitrypsin Deficiency ◽

Gene Therapy for Alpha-1 Antitrypsin Deficiency Lung Disease

Annals of the American Thoracic Society ◽

10.1513/annalsats.201506-344kv ◽

2016 ◽

Vol 13 (Supplement_4) ◽

pp. S352-S369 ◽

Cited By ~ 20

Author(s):

Maria J. Chiuchiolo ◽

Ronald G. Crystal

Keyword(s):

Gene Therapy ◽

Lung Disease ◽

Antitrypsin Deficiency ◽

Gene therapy for alpha 1-antitrypsin deficiency with an oxidant-resistant human alpha 1-antitrypsin

JCI Insight ◽

10.1172/jci.insight.135951 ◽

2020 ◽

Vol 5 (15) ◽

Cited By ~ 2

Author(s):

Meredith L. Sosulski ◽

Katie M. Stiles ◽

Esther Z. Frenk ◽

Fiona M. Hart ◽

Yuki Matsumura ◽

...

Keyword(s):

Gene Therapy ◽

Antitrypsin Deficiency ◽

S127 Gene therapy for alpha-1-antitrypsin deficiency using a pseudotyped lentivirus vector

Thorax ◽

10.1136/thoraxjnl-2015-207770.133 ◽

2015 ◽

Vol 70 (Suppl 3) ◽

pp. A72-A73 ◽

Cited By ~ 1

Author(s):

MC Paul-Smith ◽

JF Gelinas ◽

K Pytel ◽

M Chan ◽

C Meng ◽

...

Keyword(s):

Gene Therapy ◽

Lentivirus Vector ◽

Antitrypsin Deficiency ◽

181. Optimization of In Vivo Delivery of Baculovirus Gene Therapy Vectors for the Treatment of Alpha-1 Antitrypsin Deficiency

Molecular Therapy ◽

10.1016/s1525-0016(16)32990-2 ◽

2016 ◽

Vol 24 ◽

pp. S71

Author(s):

Laura vanLieshout ◽

Jondavid de Jong ◽

Jacob vanVloten ◽

Sarah K. Wootton

Keyword(s):

Gene Therapy ◽

Baculovirus Gene ◽

Gene Therapy Vectors ◽

Antitrypsin Deficiency ◽

Alpha 1 Antitrypsin ◽

In Vivo Delivery

418. Lung-Directed Gene Therapy for Human Alpha-1 Antitrypsin Deficiency Using AAV6 Vectors

Molecular Therapy ◽

10.1016/s1525-0016(16)44624-1 ◽

2007 ◽

Vol 15 ◽

pp. S161-S162

Keyword(s):

Gene Therapy ◽

Antitrypsin Deficiency ◽

Therapeutics: Gene Therapy for Alpha-1 Antitrypsin Deficiency

Methods in Molecular Biology - Alpha-1 Antitrypsin Deficiency ◽

10.1007/978-1-4939-7163-3_27 ◽

2017 ◽

pp. 267-275 ◽

Cited By ~ 3

Author(s):

Alisha M. Gruntman ◽

Terence R. Flotte

Keyword(s):

Gene Therapy ◽

Antitrypsin Deficiency ◽

Correction of the Genetic Defect in Alpha-1 Antitrypsin Deficiency by Somatic Gene Therapy

Gene Therapy for Diseases of the Lung ◽

10.1201/9781003064619-17 ◽

2020 ◽

pp. 267-283

Author(s):

Randy C. Eisensmith ◽

Savio L. C. Woo

Keyword(s):

Gene Therapy ◽

Genetic Defect ◽

Somatic Gene Therapy ◽

Somatic Gene ◽

Antitrypsin Deficiency ◽

5 Year Expression and Neutrophil Defect Repair after Gene Therapy in Alpha-1 Antitrypsin Deficiency

Molecular Therapy ◽

10.1016/j.ymthe.2017.03.029 ◽

2017 ◽

Vol 25 (6) ◽

pp. 1387-1394 ◽

Cited By ~ 43

Author(s):

Christian Mueller ◽

Gwladys Gernoux ◽

Alisha M. Gruntman ◽

Florie Borel ◽

Emer P. Reeves ◽

...

Keyword(s):

Gene Therapy ◽

Antitrypsin Deficiency ◽

Defect Repair ◽