3. Clinical outcome following 8-year enzyme replacement therapy in 884 children with type 1 Gaucher disease (GD1)

2008 ◽  
Vol 93 (2) ◽  
pp. 14
Author(s):  
Hans Andersson ◽  
Paige Kaplan ◽  
Kathrine Kacena ◽  
John Yee
Keyword(s):  
Clinical Outcome ◽  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Gaucher Disease ◽  
Enzyme Replacement ◽  
Type 1 Gaucher Disease

scholarly journals Persistent bone disease in adult type 1 Gaucher disease despite increasing doses of enzyme replacement therapy

Haematologica ◽  
2008 ◽  
Vol 93 (7) ◽  
pp. 1119-1120 ◽  
Author(s):  
M. de Fost ◽  
C. J.M. van Noesel ◽  
J. M.F.G. Aerts ◽  
M. Maas ◽  
R. G. Poll ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Bone Disease ◽  
Gaucher Disease ◽  
Adult Type ◽  
Enzyme Replacement ◽  
Type 1 Gaucher Disease

scholarly journals Cost-effectiveness of enzyme replacement therapy for type 1 Gaucher disease

2014 ◽  
Vol 9 (1) ◽  
pp. 51 ◽  
Author(s):  
Laura van Dussen ◽  
Marieke Biegstraaten ◽  
Carla EM Hollak ◽  
Marcel GW Dijkgraaf
Keyword(s):  
Cost Effectiveness ◽  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Gaucher Disease ◽  
Enzyme Replacement ◽  
Type 1 Gaucher Disease

Improvement of Splenomegaly and Pancytopenia by Enzyme Replacement Therapy Against Type 1 Gaucher Disease: A Report of Sibling Cases

2001 ◽  
Vol 73 (3) ◽  
pp. 356-362
Author(s):  
Kazuya Tsuboi ◽  
Shinsuke Iida ◽  
Miyuki Kato ◽  
Yoshihito Hayami ◽  
Ichiro Hanamura ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Gaucher Disease ◽  
Enzyme Replacement ◽  
Type 1 Gaucher Disease ◽  
Sibling Cases

Regression of skeletal changes in type 1 Gaucher disease with enzyme replacement therapy

1996 ◽  
Vol 25 (5) ◽  
pp. 485-488 ◽  
Author(s):  
Gregory M. Pastores ◽  
G. Hermann ◽  
Karen I. Norton ◽  
Mordechai Lorberboym ◽  
Robert J. Desnick
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Gaucher Disease ◽  
Enzyme Replacement ◽  
Skeletal Changes ◽  
Type 1 Gaucher Disease
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