114. Pharmacological chaperone therapy for Gaucher disease: Mechanism of action, a survey of responsive mutations and phase I clinical trial results

Molecular Genetics and Metabolism ◽

10.1016/j.ymgme.2007.10.126 ◽

2008 ◽

Vol 93 (2) ◽

pp. 44 ◽

Author(s):

Brandon Wustman ◽

Corey Pine ◽

Brian Ranes ◽

John Flanagan ◽

David Palling ◽

...

Keyword(s):

Clinical Trial ◽

Phase I ◽

Mechanism Of Action ◽

Gaucher Disease ◽

Phase I Clinical Trial ◽

Disease Mechanism ◽

Pharmacological Chaperone ◽

Clinical Trial Results

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Phase I clinical trial results of the Envoy System: a totally implantable middle ear device

Otolaryngology ◽

10.1016/s0194-5998(03)01124-0 ◽

2003 ◽

Vol 129 (2) ◽

pp. P137

Author(s):

D Chen

Keyword(s):

Clinical Trial ◽

Phase I ◽

Phase I Clinical Trial ◽

System A ◽

Clinical Trial Results

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Phase I clinical trial results of verteporfin enhanced feeder vessel therapy in subfoveal choroidal neovascularisation in age related macular degeneration

British Journal of Ophthalmology ◽

10.1136/bjo.2006.095141 ◽

2006 ◽

Vol 90 (9) ◽

pp. 1152-1156 ◽

Author(s):

I Kozak

Keyword(s):

Clinical Trial ◽

Phase I ◽

Macular Degeneration ◽

Choroidal Neovascularisation ◽

Phase I Clinical Trial ◽

Age Related Macular Degeneration ◽

Subfoveal Choroidal Neovascularisation ◽

Age Related ◽

Feeder Vessel ◽

Clinical Trial Results

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Abstract CT119: Early phase I clinical trial results for 4-demethyl-4-cholesteryloxycarbonylpenclomedine (DM-CHOC-PEN) plus radiation in cancers involving the CNS

10.1158/1538-7445.am2018-ct119 ◽

2018 ◽

Author(s):

LR Morgan ◽

T Mahmood ◽

R S. Weiner ◽

R Kawauchi ◽

M Bhandari ◽

...

Keyword(s):

Clinical Trial ◽

Phase I ◽

Early Phase ◽

Phase I Clinical Trial ◽

Clinical Trial Results

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Abstract CT101: Phase I clinical trial: results from the use of 4-demethyl-4 cholesteryloxycarbonylpenclomedine (DM-CHOC-PEN) plus radiation as treatment for cancers involving the CNS

10.1158/1538-7445.am2020-ct101 ◽

2020 ◽

Author(s):

Steven J. DiBiase ◽

Roy S. Weiner ◽

Tallat Mahmood ◽

Kendra Harris ◽

Ronald Kawauchi ◽

...

Keyword(s):

Clinical Trial ◽

Phase I ◽

Phase I Clinical Trial ◽

Clinical Trial Results

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Phase I Clinical Trial: Results From The Use Of 4-Demethyl-4-Cholesteryloxycarbonylpenclomedine (DM-CHOC-PEN) Plus Radiation As Treatment For Cancers Involving The CNS

International Journal of Radiation Oncology*Biology*Physics ◽

10.1016/j.ijrobp.2020.07.092 ◽

2020 ◽

Vol 108 (3) ◽

pp. e716-e717

Author(s):

S.J. DiBiase ◽

R. Weiner ◽

T. Mahmood ◽

K. Harris ◽

A. Baghian ◽

...

Keyword(s):

Clinical Trial ◽

Phase I ◽

Phase I Clinical Trial ◽

Clinical Trial Results

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Phase I clinical trial results of aceneuramic acid for GNE myopathy in Japan

Translational Medicine Communications ◽

10.1186/s41231-018-0025-0 ◽

2018 ◽

Vol 3 (1) ◽

Author(s):

Naoki Suzuki ◽

Masaaki Kato ◽

Hitoshi Warita ◽

Rumiko Izumi ◽

Maki Tateyama ◽

...

Keyword(s):

Clinical Trial ◽

Phase I ◽

Phase I Clinical Trial ◽

Gne Myopathy ◽

Clinical Trial Results

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Phase I Clinical Trial of a Genetically Modified and Oncolytic Vaccinia Virus GL-ONC1 in patients with peritoneal carcinomatosis

Zeitschrift für Gastroenterologie ◽

10.1055/s-0032-1324086 ◽

2012 ◽

Vol 50 (08) ◽

Author(s):

UM Lauer ◽

M Zimmermann ◽

U Koppenhöfer ◽

M Bitzer ◽

NP Malek ◽

...

Keyword(s):

Clinical Trial ◽

Phase I ◽

Vaccinia Virus ◽

Peritoneal Carcinomatosis ◽

Genetically Modified ◽

Phase I Clinical Trial

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SAFETY OF A NEW CUBAN PNEUMOCOCCAL CONJUGATE VACCINE: A PHASE I CLINICAL TRIAL IN INFANTS 7 MONTH-OLD

10.26226/morressier.5731f0d7d462b8029237fd99 ◽

2016 ◽

Author(s):

Rinaldo Puga-Gomez

Keyword(s):

Clinical Trial ◽

Phase I ◽

Conjugate Vaccine ◽

Pneumococcal Conjugate Vaccine ◽

Phase I Clinical Trial

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Faculty Opinions recommendation of Phase I clinical trial of a selective inhibitor of CYP17, abiraterone acetate, confirms that castration-resistant prostate cancer commonly remains hormone driven.

Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature ◽

10.3410/f.1118816.793494158 ◽

2014 ◽

Author(s):

Thomas Flaig

Keyword(s):

Prostate Cancer ◽

Clinical Trial ◽

Phase I ◽

Abiraterone Acetate ◽

Selective Inhibitor ◽

Phase I Clinical Trial ◽

Castration Resistant Prostate Cancer ◽

Castration Resistant

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Faculty Opinions recommendation of A phase I clinical trial of Ad5/3-Δ24, a novel serotype-chimeric, infectivity-enhanced, conditionally-replicative adenovirus (CRAd), in patients with recurrent ovarian cancer.

Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature ◽

10.3410/f.718026292.793481389 ◽

2013 ◽

Author(s):

Steve Plaxe ◽

Kristy Ward

Keyword(s):

Ovarian Cancer ◽

Clinical Trial ◽

Phase I ◽

Recurrent Ovarian Cancer ◽

Phase I Clinical Trial ◽

Conditionally Replicative Adenovirus

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