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Agalsidase alfa in pediatric patients with Fabry disease: A 7-year open-label study
Molecular Genetics and Metabolism
◽
10.1016/j.ymgme.2012.11.217
◽
2013
◽
Vol 108
(2)
◽
pp. S81-S82
Author(s):
Raphael Schiffmann
◽
Gregory Pastores
◽
Chang Peter
◽
Martin Rick
◽
Wijatyk Anna
Keyword(s):
Fabry Disease
◽
Pediatric Patients
◽
Open Label
◽
Open Label Study
◽
Label Study
◽
Agalsidase Alfa
Download Full-text
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Switching from agalsidase alfa to pegunigalsidase alfa to treat patients with Fabry disease: 1 year of treatment data from BRIDGE, a phase 3 open-label study
Molecular Genetics and Metabolism
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10.1016/j.ymgme.2020.12.147
◽
2021
◽
Vol 132
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◽
pp. S65
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◽
Gabriela Dostalova
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Fabry Disease
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Phase 3
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Open Label Study
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Label Study
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Agalsidase Alfa
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Switching from agalsidase alfa to pegunigalsidase alfa for treating Fabry disease: One year of treatment data from BRIDGE, a phase III open label study
Molecular Genetics and Metabolism
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10.1016/j.ymgme.2019.11.249
◽
2020
◽
Vol 129
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◽
pp. S98-S99
Author(s):
Ales Linhart
◽
Gabriela Dostalova
◽
Kathy Nicholls
◽
Michael West
◽
Camilla Tøndel
◽
...
Keyword(s):
Fabry Disease
◽
Phase Iii
◽
Open Label
◽
Open Label Study
◽
Label Study
◽
Agalsidase Alfa
◽
Treatment Data
◽
One Year
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Safety and Efficacy of Enzyme Replacement Therapy with Agalsidase Beta: An International, Open-label Study in Pediatric Patients with Fabry Disease
The Journal of Pediatrics
◽
10.1016/j.jpeds.2007.09.007
◽
2008
◽
Vol 152
(4)
◽
pp. 563-570.e1
◽
Cited By ~ 94
Author(s):
J. Edmond Wraith
◽
Anna Tylki-Szymanska
◽
Nathalie Guffon
◽
Y. Howard Lien
◽
Michel Tsimaratos
◽
...
Keyword(s):
Enzyme Replacement Therapy
◽
Fabry Disease
◽
Replacement Therapy
◽
Pediatric Patients
◽
Agalsidase Beta
◽
Open Label
◽
Open Label Study
◽
Label Study
◽
Safety And Efficacy
◽
Enzyme Replacement
Download Full-text
Results of a phase 2, multicenter, single‐arm, open‐label study of lenalidomide in pediatric patients with relapsed or refractory acute myeloid leukemia
Pediatric Blood & Cancer
◽
10.1002/pbc.28946
◽
2021
◽
Author(s):
Maureen M. O'Brien
◽
Todd A. Alonzo
◽
Todd M. Cooper
◽
John E. Levine
◽
Patrick A. Brown
◽
...
Keyword(s):
Acute Myeloid Leukemia
◽
Myeloid Leukemia
◽
Pediatric Patients
◽
Phase 2
◽
Open Label
◽
Open Label Study
◽
Label Study
◽
Refractory Acute Myeloid Leukemia
◽
Acute Myeloid
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Aripiprazole in the Treatment of Irritability in Pediatric Patients (Aged 6–17 Years) with Autistic Disorder: Results from a 52-Week, Open-Label Study
Journal of Child and Adolescent Psychopharmacology
◽
10.1089/cap.2009.0121
◽
2011
◽
Vol 21
(3)
◽
pp. 229-236
◽
Cited By ~ 46
Author(s):
Ronald N. Marcus
◽
Randall Owen
◽
George Manos
◽
Raymond Mankoski
◽
Lisa Kamen
◽
...
Keyword(s):
Autistic Disorder
◽
Pediatric Patients
◽
Open Label
◽
Open Label Study
◽
Label Study
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Su1923 Pharmacokinetics and Exposure-Response Relationships of Golimumab in Pediatric Patients With Moderate to Severe Ulcerative Colitis: Results From a Multicenter Open Label Study
Gastroenterology
◽
10.1016/s0016-5085(16)32022-4
◽
2016
◽
Vol 150
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◽
pp. S590
◽
Cited By ~ 2
Author(s):
Omoniyi J. Adedokun
◽
Daphne Chan
◽
Lakshmi Padgett
◽
Yan Xu
◽
Jeffrey S. Hyams
◽
...
Keyword(s):
Ulcerative Colitis
◽
Pediatric Patients
◽
Open Label
◽
Open Label Study
◽
Label Study
◽
Severe Ulcerative Colitis
◽
Exposure Response
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W1178 Clinical Efficacy and Safety of Mesalamine Suppositories in the Treatment of Pediatric Patients with Ulcerative Proctitis: A Multicenter, Open-Label Study
Gastroenterology
◽
10.1016/s0016-5085(09)63091-2
◽
2009
◽
Vol 136
(5)
◽
pp. A-671
Author(s):
Melvin B. Heyman
◽
Jaroslaw Kierkus
◽
Jean Spénard
◽
Monique Giguere
Keyword(s):
Clinical Efficacy
◽
Pediatric Patients
◽
Efficacy And Safety
◽
Open Label
◽
Open Label Study
◽
Label Study
◽
Ulcerative Proctitis
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Pharmacokinetics and safety of apremilast in pediatric patients with moderate to severe plaque psoriasis: Results from a phase 2 open-label study
Journal of the American Academy of Dermatology
◽
10.1016/j.jaad.2019.08.019
◽
2020
◽
Vol 82
(2)
◽
pp. 389-397
◽
Cited By ~ 7
Author(s):
Amy S. Paller
◽
Ying Hong
◽
Emily M. Becker
◽
Raul de Lucas
◽
Maria Paris
◽
...
Keyword(s):
Plaque Psoriasis
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Pediatric Patients
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Phase 2
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Open Label
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Open Label Study
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Label Study
◽
Severe Plaque Psoriasis
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Clinical Outcomes from an Open-Label Study of Edivoxetine Use in Pediatric Patients with Attention-Deficit/Hyperactivity Disorder
Journal of Child and Adolescent Psychopharmacology
◽
10.1089/cap.2012.0016
◽
2013
◽
Vol 23
(3)
◽
pp. 200-207
◽
Cited By ~ 8
Author(s):
Ling Jin
◽
Wen Xu
◽
David Krefetz
◽
Daniel Gruener
◽
William Kielbasa
◽
...
Keyword(s):
Attention Deficit Hyperactivity Disorder
◽
Clinical Outcomes
◽
Attention Deficit
◽
Pediatric Patients
◽
Open Label
◽
Open Label Study
◽
Label Study
◽
Hyperactivity Disorder
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Safety and efficacy of apremilast in pediatric patients with moderate to severe plaque psoriasis: Results from a phase 2 open-label study
Journal of the American Academy of Dermatology
◽
10.1016/j.jaad.2019.06.455
◽
2019
◽
Vol 81
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◽
pp. AB120
Keyword(s):
Plaque Psoriasis
◽
Pediatric Patients
◽
Phase 2
◽
Open Label
◽
Open Label Study
◽
Label Study
◽
Safety And Efficacy
◽
Severe Plaque Psoriasis
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