scholarly journals Coordinated β-globin expression and α2-globin reduction in a multiplex lentiviral gene therapy vector for β-thalassemia

2021 ◽  
Author(s):  
Tiwaporn Nualkaew ◽  
Karine Sii-Felice ◽  
Marie Giorgi ◽  
Bradley McColl ◽  
Julie Gouzil ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Gene Therapy Vector ◽  
Globin Reduction ◽  
Lentiviral Gene Therapy

scholarly journals Lentiviral gene therapy vector with UCOE stably restores function in iPSC-derived neutrophils of a CDG patient

Matters ◽  
2018 ◽  
Author(s):  
Walther Haenseler ◽  
Elena Kuzmenko ◽  
Adjoa Smalls-Mantey ◽  
Cathy Browne ◽  
Reinhard Seger ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Gene Therapy Vector ◽  
Lentiviral Gene Therapy

scholarly journals Corrigendum to “Oncogenesis Following Delivery of a Nonprimate Lentiviral Gene Therapy Vector to Fetal and Neonatal Mice”

2006 ◽  
Vol 13 (4) ◽  
pp. 830 ◽  
Author(s):  
Mike Themis ◽  
Simon N. Waddington ◽  
Manfred Schmidt ◽  
Christof von Kalle ◽  
Yoahe Wang ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Gene Therapy Vector ◽  
Neonatal Mice ◽  
Lentiviral Gene Therapy

scholarly journals Oncogenesis Following Delivery of a Nonprimate Lentiviral Gene Therapy Vector to Fetal and Neonatal Mice

2005 ◽  
Vol 12 (4) ◽  
pp. 763-771 ◽  
Author(s):  
Mike Themis ◽  
Simon N. Waddington ◽  
Manfred Schmidt ◽  
Christof von Kalle ◽  
Yoahe Wang ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Gene Therapy Vector ◽  
Neonatal Mice ◽  
Lentiviral Gene Therapy

scholarly journals Development of downstream purification process for lentiviral gene therapy vector

2020 ◽  
Author(s):  
Ronit Ghosh ◽  
Sneha Gopal ◽  
Jonathan Dordick ◽  
Koley Sushmita ◽  
Steven Cramer
Keyword(s):  
Gene Therapy ◽  
Purification Process ◽  
Gene Therapy Vector ◽  
Lentiviral Gene Therapy

A novel gene therapy vector based on hyaluronic acid and solid lipid nanoparticles for ocular diseases

2014 ◽  
Vol 465 (1-2) ◽  
pp. 413-426 ◽  
Author(s):  
Paola Stephanie Apaolaza ◽  
Diego Delgado ◽  
Ana del Pozo-Rodríguez ◽  
Alicia Rodríguez Gascón ◽  
M.Ángeles Solinís
Keyword(s):  
Gene Therapy ◽  
Hyaluronic Acid ◽  
Solid Lipid Nanoparticles ◽  
Lipid Nanoparticles ◽  
Ocular Diseases ◽  
Gene Therapy Vector ◽  
Solid Lipid ◽  
Novel Gene

scholarly journals Lentiviral Gene Therapy for X-Linked Chronic Granulomatous Disease

PEDIATRICS ◽  
2020 ◽  
Vol 146 (Supplement 4) ◽  
pp. S380.2-S381
Author(s):  
Mamatha Mandava ◽  
Kelli W. Williams
Keyword(s):  
Gene Therapy ◽  
Chronic Granulomatous Disease ◽  
Granulomatous Disease ◽  
Lentiviral Gene Therapy
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