The pheNIX trial: first-in-human gene therapy trial for PKU due to phenylalanine hydroxylase (PAH) deficiency

2021 ◽  
Vol 132 ◽  
pp. S166-S167
Author(s):  
Janet Iles ◽  
Olaf Bodamer ◽  
Barbara Burton ◽  
Gabriel Cohn ◽  
Yvonne White ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Phenylalanine Hydroxylase ◽  
Human Gene ◽  
Human Gene Therapy ◽  
Gene Therapy Trial ◽  
Therapy Trial

scholarly journals Initial results from a first-in-human gene therapy trial on X-linked retinitis pigmentosa caused by mutations in RPGR

2020 ◽  
Vol 26 (3) ◽  
pp. 354-359 ◽  
Author(s):  
Jasmina Cehajic-Kapetanovic ◽  
Kanmin Xue ◽  
Cristina Martinez-Fernandez de la Camara ◽  
Anika Nanda ◽  
Alexandra Davies ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Retinitis Pigmentosa ◽  
Human Gene ◽  
Human Gene Therapy ◽  
Gene Therapy Trial ◽  
Therapy Trial ◽  
Initial Results

Liability Considerations Presented by Human Gene Therapy

1991 ◽  
Vol 2 (3) ◽  
pp. 235-242 ◽  
Author(s):  
Julie Gage Palmer
Keyword(s):  
Gene Therapy ◽  
Human Gene ◽  
Human Gene Therapy
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