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Challenges and Prospects for Alpha-1 Antitrypsin Deficiency Gene Therapy
Human Gene Therapy
◽
10.1089/hum.2015.044
◽
2015
◽
Vol 26
(11)
◽
pp. 709-718
◽
Cited By ~ 13
Author(s):
Joanna Wozniak
◽
Tomasz Wandtke
◽
Piotr Kopinski
◽
Joanna Chorostowska-Wynimko
Keyword(s):
Gene Therapy
◽
Antitrypsin Deficiency
◽
Alpha 1 Antitrypsin Deficiency
◽
Deficiency Gene
◽
Alpha 1 Antitrypsin
Download Full-text
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References
Gene Therapy for Alpha-1-Antitrypsin Deficiency Diseases
Gene Therapy Applications
◽
10.5772/17415
◽
2011
◽
Author(s):
Parveen Salahuddin
Keyword(s):
Gene Therapy
◽
Antitrypsin Deficiency
◽
Alpha 1 Antitrypsin Deficiency
◽
Alpha 1 Antitrypsin
◽
Deficiency Diseases
Download Full-text
DNA diagnostics and approaches to gene therapy of hereditary α1-antitrypsin deficiency
Biopolymers and Cell
◽
10.7124/bc.000247
◽
1990
◽
Vol 6
(1)
◽
pp. 51-56
Author(s):
A. L. Schwartzman
◽
M. P. Strakhova
◽
V. S. Gaitskhoki
◽
W. Berger
◽
Ch. Coutelle
Keyword(s):
Gene Therapy
◽
Dna Diagnostics
◽
Antitrypsin Deficiency
◽
Alpha 1 Antitrypsin Deficiency
◽
Alpha 1 Antitrypsin
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Gene Therapy for Alpha-1 Antitrypsin Deficiency Lung Disease
Annals of the American Thoracic Society
◽
10.1513/annalsats.201506-344kv
◽
2016
◽
Vol 13
(Supplement_4)
◽
pp. S352-S369
◽
Cited By ~ 20
Author(s):
Maria J. Chiuchiolo
◽
Ronald G. Crystal
Keyword(s):
Gene Therapy
◽
Lung Disease
◽
Antitrypsin Deficiency
◽
Alpha 1 Antitrypsin Deficiency
◽
Alpha 1 Antitrypsin
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Gene therapy for alpha 1-antitrypsin deficiency with an oxidant-resistant human alpha 1-antitrypsin
JCI Insight
◽
10.1172/jci.insight.135951
◽
2020
◽
Vol 5
(15)
◽
Cited By ~ 2
Author(s):
Meredith L. Sosulski
◽
Katie M. Stiles
◽
Esther Z. Frenk
◽
Fiona M. Hart
◽
Yuki Matsumura
◽
...
Keyword(s):
Gene Therapy
◽
Antitrypsin Deficiency
◽
Alpha 1 Antitrypsin Deficiency
◽
Alpha 1 Antitrypsin
Download Full-text
Intrapleural Administration of a Second-Generation Oxidation Resistant Alpha 1-Antitrypsin Gene Therapy for Alpha 1-Antitrypsin Deficiency
10.1164/ajrccm-conference.2020.201.1_meetingabstracts.a2284
◽
2020
◽
Author(s):
K.M. Stiles
◽
M.L. Sosulski
◽
B.P. De
◽
S.R. Driscoll
◽
S.M. Kaminsky
◽
...
Keyword(s):
Gene Therapy
◽
Second Generation
◽
Antitrypsin Deficiency
◽
Alpha 1 Antitrypsin Deficiency
◽
Oxidation Resistant
◽
Alpha 1 Antitrypsin
◽
Intrapleural Administration
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S127 Gene therapy for alpha-1-antitrypsin deficiency using a pseudotyped lentivirus vector
Thorax
◽
10.1136/thoraxjnl-2015-207770.133
◽
2015
◽
Vol 70
(Suppl 3)
◽
pp. A72-A73
◽
Cited By ~ 1
Author(s):
MC Paul-Smith
◽
JF Gelinas
◽
K Pytel
◽
M Chan
◽
C Meng
◽
...
Keyword(s):
Gene Therapy
◽
Lentivirus Vector
◽
Antitrypsin Deficiency
◽
Alpha 1 Antitrypsin Deficiency
◽
Alpha 1 Antitrypsin
Download Full-text
181. Optimization of In Vivo Delivery of Baculovirus Gene Therapy Vectors for the Treatment of Alpha-1 Antitrypsin Deficiency
Molecular Therapy
◽
10.1016/s1525-0016(16)32990-2
◽
2016
◽
Vol 24
◽
pp. S71
Author(s):
Laura vanLieshout
◽
Jondavid de Jong
◽
Jacob vanVloten
◽
Sarah K. Wootton
Keyword(s):
Gene Therapy
◽
Baculovirus Gene
◽
Gene Therapy Vectors
◽
Antitrypsin Deficiency
◽
Alpha 1 Antitrypsin Deficiency
◽
Alpha 1 Antitrypsin
◽
In Vivo Delivery
Download Full-text
418. Lung-Directed Gene Therapy for Human Alpha-1 Antitrypsin Deficiency Using AAV6 Vectors
Molecular Therapy
◽
10.1016/s1525-0016(16)44624-1
◽
2007
◽
Vol 15
◽
pp. S161-S162
Keyword(s):
Gene Therapy
◽
Antitrypsin Deficiency
◽
Alpha 1 Antitrypsin Deficiency
◽
Alpha 1 Antitrypsin
Download Full-text
Therapeutics: Gene Therapy for Alpha-1 Antitrypsin Deficiency
Methods in Molecular Biology - Alpha-1 Antitrypsin Deficiency
◽
10.1007/978-1-4939-7163-3_27
◽
2017
◽
pp. 267-275
◽
Cited By ~ 3
Author(s):
Alisha M. Gruntman
◽
Terence R. Flotte
Keyword(s):
Gene Therapy
◽
Antitrypsin Deficiency
◽
Alpha 1 Antitrypsin Deficiency
◽
Alpha 1 Antitrypsin
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Correction of the Genetic Defect in Alpha-1 Antitrypsin Deficiency by Somatic Gene Therapy
Gene Therapy for Diseases of the Lung
◽
10.1201/9781003064619-17
◽
2020
◽
pp. 267-283
Author(s):
Randy C. Eisensmith
◽
Savio L. C. Woo
Keyword(s):
Gene Therapy
◽
Genetic Defect
◽
Somatic Gene Therapy
◽
Somatic Gene
◽
Antitrypsin Deficiency
◽
Alpha 1 Antitrypsin Deficiency
◽
Alpha 1 Antitrypsin
Download Full-text
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