Age-Dependent Effect of Myostatin Blockade on Disease Severity in a Murine Model of Limb-Girdle Muscular Dystrophy

Dependent Effect ◽

Age Dependent

Autologous intramuscular transplantation of engineered satellite cells induces exosome-mediated systemic expression of Fukutin-related protein and rescues disease phenotype in a murine model of limb-girdle muscular dystrophy type 2I

Human Molecular Genetics ◽

10.1093/hmg/ddx252 ◽

2017 ◽

Vol 26 (19) ◽

pp. 3682-3698 ◽

Cited By ~ 11

Author(s):

Paola Frattini ◽

Chiara Villa ◽

Francesca De Santis ◽

Mirella Meregalli ◽

Marzia Belicchi ◽

...

Keyword(s):

Muscular Dystrophy ◽

Satellite Cells ◽

Murine Model ◽

Disease Phenotype ◽

Related Protein

294. Restriction of Calpain3 Expression to the Skeletal Muscle Prevents Cardiac Toxicity and Corrects Pathology in a Murine Model of Limb-Girdle Muscular Dystrophy

Molecular Therapy ◽

10.1016/s1525-0016(16)34629-9 ◽

2013 ◽

Vol 21 ◽

pp. S112

Keyword(s):

Skeletal Muscle ◽

Muscular Dystrophy ◽

Murine Model ◽

Cardiac Toxicity ◽

Restriction of Calpain3 Expression to the Skeletal Muscle Prevents Cardiac Toxicity and Corrects Pathology in a Murine Model of Limb-Girdle Muscular Dystrophy

Circulation ◽

10.1161/circulationaha.113.001340 ◽

2013 ◽

Vol 128 (10) ◽

pp. 1094-1104 ◽

Cited By ~ 23

Author(s):

Carinne Roudaut ◽

Florence Le Roy ◽

Laurence Suel ◽

Jérôme Poupiot ◽

Karine Charton ◽

...

Keyword(s):

Skeletal Muscle ◽

Muscular Dystrophy ◽

Murine Model ◽

Cardiac Toxicity ◽

377. AAV-Mediated Transfer of FKRP Shows Therapeutic Efficacy in a Murine Model of Limb-Girdle Muscular Dystrophy Type 2i, but Requires Tight Control of Gene Expression

Molecular Therapy ◽

10.1016/s1525-0016(16)33186-0 ◽

2016 ◽

Vol 24 ◽

pp. S150

Author(s):

Evelyne Gicquel ◽

Natacha Maizonnier ◽

Steven J. Foltz ◽

William Martin ◽

Nathalie Bourg ◽

...

Keyword(s):

Gene Expression ◽

Muscular Dystrophy ◽

Murine Model ◽

Therapeutic Efficacy ◽

Tight Control ◽

Control Of Gene Expression

Myostatin blockade improves function but not histopathology in a murine model of limb-girdle muscular dystrophy 2C

Muscle & Nerve ◽

10.1002/mus.20920 ◽

2008 ◽

Vol 37 (3) ◽

pp. 308-316 ◽

Cited By ~ 50

Author(s):

Sasha Bogdanovich ◽

Elizabeth M. McNally ◽

Tejvir S. Khurana

Keyword(s):

Muscular Dystrophy ◽

Murine Model ◽

Correlation between morphological and electro-physiological features in limb-girdle muscular dystrophy

Electroencephalography and Clinical Neurophysiology ◽

10.1016/s0013-4694(97)88200-8 ◽

1997 ◽

Vol 103 (1) ◽

pp. 65

Author(s):

S Groppa

Keyword(s):

Muscular Dystrophy ◽

Investigating The Regulation And Role Of P38 Mapk In Collagen-Related Limb Girdle Muscular Dystrophy

10.30707/etd2020.1606247535.293019ap ◽

2020 ◽

Author(s):

Briseida Oceguera-Perez

Keyword(s):

Muscular Dystrophy ◽

P38 Mapk ◽

Orphan designation: 505 amino acid protein, corresponding to amino acids 2-506 of the wild-type human histidyl-tRNA synthetase, Treatment of limb-girdle muscular dystrophy

Case Medical Research ◽

10.31525/cmr-2935ce2 ◽

2020 ◽

Author(s):

Keyword(s):

Amino Acids ◽

Amino Acid ◽

Muscular Dystrophy ◽

Trna Synthetase ◽

Wild Type ◽

Orphan Designation ◽

Acid Protein ◽

Amino Acid Protein

Limb-Girdle Muscular Dystrophy Type 2I in Norway

Case Medical Research ◽

10.31525/ct1-nct03930628 ◽

2019 ◽

Author(s):

Keyword(s):

Muscular Dystrophy ◽

Defining Clinical Endpoints in Limb Girdle Muscular Dystrophy (LGMD)

Case Medical Research ◽

10.31525/ct1-nct03981289 ◽

2019 ◽

Author(s):

Keyword(s):

Muscular Dystrophy ◽

Clinical Endpoints