Orphan designation: Adeno-associated virus serotype HSC15 expressing human phenylalanine hydroxylase, Treatment of phenylalanine hydroxylase deficiency
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1999 ◽
Vol 135
(3)
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pp. 375-378
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2013 ◽
Vol 32
(4)
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pp. S250-S251
2015 ◽
Vol 990
◽
pp. 15-22
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