Gene therapy for recessive dystrophic epidermolysis bullosa

Chinese Journal of Dermatology ◽

10.35541/cjd.20210499 ◽

2021 ◽

Keyword(s):

Gene Therapy ◽

Epidermolysis Bullosa ◽

Dystrophic Epidermolysis Bullosa ◽

Recessive Dystrophic Epidermolysis Bullosa

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The potential of gene therapy for recessive dystrophic epidermolysis bullosa

British Journal of Dermatology ◽

10.1111/bjd.20910 ◽

2021 ◽

Author(s):

K.S. Subramaniam ◽

M.N. Antoniou ◽

J.A. McGrath ◽

S.M. Lwin

Keyword(s):

Gene Therapy ◽

Epidermolysis Bullosa ◽

Dystrophic Epidermolysis Bullosa ◽

Recessive Dystrophic Epidermolysis Bullosa

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The road to gene therapy for recessive dystrophic epidermolysis bullosa

Cell and Gene Therapy Insights ◽

10.18609/cgti.2017.011 ◽

2017 ◽

Vol 3 (2) ◽

pp. 75-81

Author(s):

Peter M Marinkovich ◽

Ngon T Nguyen ◽

Zurab Siprashvili

Keyword(s):

Gene Therapy ◽

Epidermolysis Bullosa ◽

Dystrophic Epidermolysis Bullosa ◽

The Road ◽

Recessive Dystrophic Epidermolysis Bullosa

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Construction of Skin Equivalents for Gene Therapy of Recessive Dystrophic Epidermolysis Bullosa

Human Gene Therapy ◽

10.1089/hum.2004.15.921 ◽

2004 ◽

Vol 15 (10) ◽

pp. 921-933 ◽

Author(s):

Yannick Gache ◽

Christine Baldeschi ◽

Marcela Del Rio ◽

Laurent Gagnoux-Palacios ◽

Fernando larcher ◽

...

Keyword(s):

Gene Therapy ◽

Epidermolysis Bullosa ◽

Dystrophic Epidermolysis Bullosa ◽

Skin Equivalents ◽

Recessive Dystrophic Epidermolysis Bullosa

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Patient pre-selection outcomes for the European GENEGRAFT ex vivo phase I/II gene therapy trial for recessive dystrophic epidermolysis bullosa.

10.26226/morressier.595a9c56d462b80296c9fadf ◽

2017 ◽

Author(s):

Su Lwin

Keyword(s):

Gene Therapy ◽

Phase I ◽

Epidermolysis Bullosa ◽

Ex Vivo ◽

Dystrophic Epidermolysis Bullosa ◽

Gene Therapy Trial ◽

Recessive Dystrophic Epidermolysis Bullosa ◽

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Translating the combination of gene therapy and tissue engineering for treating recessive dystrophic epidermolysis bullosa

10.22203/ecm.v035a06 ◽

2018 ◽

Vol 35 ◽

pp. 73-86 ◽

Author(s):

A Dakiw Piaceski ◽

◽

D Larouche ◽

K Ghani ◽

F Bisson ◽

...

Keyword(s):

Tissue Engineering ◽

Gene Therapy ◽

Epidermolysis Bullosa ◽

Dystrophic Epidermolysis Bullosa ◽

Recessive Dystrophic Epidermolysis Bullosa

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EBGene trial: patient preselection outcomes for the European GENEGRAFT ex vivo phase I/II gene therapy trial for recessive dystrophic epidermolysis bullosa

British Journal of Dermatology ◽

10.1111/bjd.18559 ◽

2019 ◽

Vol 182 (3) ◽

pp. 794-797 ◽

Author(s):

S. Gaucher ◽

S.M. Lwin ◽

M. Titeux ◽

A. Abdul‐Wahab ◽

N. Pironon ◽

...

Keyword(s):

Gene Therapy ◽

Phase I ◽

Epidermolysis Bullosa ◽

Ex Vivo ◽

Dystrophic Epidermolysis Bullosa ◽

Gene Therapy Trial ◽

Recessive Dystrophic Epidermolysis Bullosa ◽

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SIN Retroviral Vectors Expressing COL7A1 Under Human Promoters for Ex Vivo Gene Therapy of Recessive Dystrophic Epidermolysis Bullosa

Molecular Therapy ◽

10.1038/mt.2010.91 ◽

2010 ◽

Vol 18 (8) ◽

pp. 1509-1518 ◽

Author(s):

Matthias Titeux ◽

Valérie Pendaries ◽

Maria A Zanta-Boussif ◽

Audrey Décha ◽

Nathalie Pironon ◽

...

Keyword(s):

Gene Therapy ◽

Epidermolysis Bullosa ◽

Ex Vivo ◽

Retroviral Vectors ◽

Dystrophic Epidermolysis Bullosa ◽

Ex Vivo Gene Therapy ◽

Recessive Dystrophic Epidermolysis Bullosa

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Phase I/II Ex Vivo Gene Therapy Clinical Trial for Recessive Dystrophic Epidermolysis Bullosa Using Skin Equivalent Grafts Genetically Corrected with a COL7A1-Encoding SIN Retroviral Vector (GENEGRAFT)

Human Gene Therapy Clinical Development ◽

10.1089/humc.2014.2508 ◽

2014 ◽

Vol 25 (2) ◽

pp. 65-66 ◽

Keyword(s):

Clinical Trial ◽

Gene Therapy ◽

Phase I ◽

Epidermolysis Bullosa ◽

Ex Vivo ◽

Retroviral Vector ◽

Dystrophic Epidermolysis Bullosa ◽

Ex Vivo Gene Therapy ◽

Recessive Dystrophic Epidermolysis Bullosa ◽

Therapy Clinical Trial

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398 A simple, efficient non-viral gene therapy for recessive dystrophic epidermolysis bullosa

Journal of Investigative Dermatology ◽

10.1016/j.jid.2016.02.432 ◽

2016 ◽

Vol 136 (5) ◽

pp. S70

Author(s):

L. Cutlar ◽

D. Zhou ◽

X. Hu ◽

B. Duarte ◽

F. Larcher ◽

...

Keyword(s):

Gene Therapy ◽

Epidermolysis Bullosa ◽

Dystrophic Epidermolysis Bullosa ◽

Viral Gene Therapy ◽

Recessive Dystrophic Epidermolysis Bullosa

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Immune reactivity to type VII collagen: implications for gene therapy of recessive dystrophic epidermolysis bullosa

Gene Therapy ◽

10.1038/gt.2010.36 ◽

2010 ◽

Vol 17 (7) ◽

pp. 930-937 ◽

Author(s):

V Pendaries ◽

G Gasc ◽

M Titeux ◽

C Leroux ◽

Z G Vitezica ◽

...

Keyword(s):

Gene Therapy ◽

Epidermolysis Bullosa ◽

Immune Reactivity ◽

Dystrophic Epidermolysis Bullosa ◽

Type Vii Collagen ◽

Recessive Dystrophic Epidermolysis Bullosa

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