Use of real‐world evidence in regulatory decisions for rare diseases in the United States—Current status and future directions

Jasmanda Wu; Cunlin Wang; Sengwee Toh; Federica Edith Pisa; Larry Bauer

doi:10.1002/pds.4962

Use of real‐world evidence in regulatory decisions for rare diseases in the United States—Current status and future directions

Pharmacoepidemiology and Drug Safety ◽

10.1002/pds.4962 ◽

2020 ◽

Vol 29 (10) ◽

pp. 1213-1218 ◽

Cited By ~ 1

Author(s):

Jasmanda Wu ◽

Cunlin Wang ◽

Sengwee Toh ◽

Federica Edith Pisa ◽

Larry Bauer

Keyword(s):

United States ◽

Rare Diseases ◽

Real World ◽

The United States ◽

Current Status ◽

Future Directions ◽

Real World Evidence ◽

Regulatory Decisions

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Current Status and Future Directions for Library and Archive Conservation Education in the United States

Restaurator International Journal for the Preservation of Library and Archival Material ◽

10.1515/res-2019-0025 ◽

2019 ◽

Vol 40 (3-4) ◽

pp. 331-335

Author(s):

Theresa J. Smith

Keyword(s):

United States ◽

The United States ◽

Conservation Education ◽

Current Status ◽

Future Directions

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Real‐World Evidence of Treatment, Tolerance, Healthcare Utilization, and Costs Among Postacute Care Adult Patients Receiving Enteral Peptide‐Based Diets in the United States

Journal of Parenteral and Enteral Nutrition ◽

10.1002/jpen.2074 ◽

2021 ◽

Author(s):

Chris LaVallee ◽

Prafullakumar Seelam ◽

Santosh Balakrishnan ◽

Cynthia Lowen ◽

Aimee Henrikson ◽

...

Keyword(s):

United States ◽

Healthcare Utilization ◽

Real World ◽

The United States ◽

Adult Patients ◽

Real World Evidence ◽

Postacute Care ◽

Treatment Tolerance

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Su1769 REAL-WORLD EVIDENCE ON PREVALENCE OF GASTROPARESIS IN ADULTS: A NATIONAL LARGE-SCALED SECONDARY DATABASE ANALYSIS FROM THE UNITED STATES

Gastroenterology ◽

10.1016/s0016-5085(20)32297-6 ◽

2020 ◽

Vol 158 (6) ◽

pp. S-640-S-641

Author(s):

Yizhou Ye ◽

Yu Yin ◽

Dimitri Bennett ◽

Cristina Almansa

Keyword(s):

United States ◽

Real World ◽

The United States ◽

Database Analysis ◽

Secondary Database ◽

Real World Evidence

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O-026 Real world evidence for acute stroke thrombectomy in the united states from the neurovascular quality initiative-quality outcomes database

10.1136/neurintsurg-2020-snis.26 ◽

2020 ◽

Author(s):

R Abdalla ◽

D Cantrell ◽

M Potts ◽

B Jahromi ◽

A Shaibani ◽

...

Keyword(s):

United States ◽

Acute Stroke ◽

Real World ◽

The United States ◽

Quality Outcomes ◽

Real World Evidence

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Systematic Literature Review of Real-World Evidence on Adherence with Biologics in Inflammatory Bowel Disease in the United States

Value in Health ◽

10.1016/j.jval.2018.04.581 ◽

2018 ◽

Vol 21 ◽

pp. S87

Author(s):

E Rupniewska ◽

D Singer ◽

S Khan ◽

M Neighbors ◽

JA Chiarappa ◽

...

Keyword(s):

United States ◽

Inflammatory Bowel Disease ◽

Literature Review ◽

Systematic Literature Review ◽

Real World ◽

Bowel Disease ◽

The United States ◽

Real World Evidence ◽

Inflammatory Bowel

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PNS38 Can Real-World Evidence Drive Policy Decisions: A Comparison of the United States and Europe

Value in Health ◽

10.1016/j.jval.2021.04.893 ◽

2021 ◽

Vol 24 ◽

pp. S179

Author(s):

V. Trivedi ◽

M. Namjoshi

Keyword(s):

United States ◽

Real World ◽

The United States ◽

Policy Decisions ◽

Real World Evidence

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Real-world evidence of stroke prevention in patients with nonvalvular atrial fibrillation in the United States: the REVISIT-US study

Current Medical Research and Opinion ◽

10.1080/03007995.2016.1237937 ◽

2016 ◽

Vol 32 (12) ◽

pp. 2047-2053 ◽

Cited By ~ 62

Author(s):

Craig I. Coleman ◽

Matthias Antz ◽

Kevin Bowrin ◽

Thomas Evers ◽

Edgar P. Simard ◽

...

Keyword(s):

United States ◽

Atrial Fibrillation ◽

Real World ◽

Stroke Prevention ◽

The United States ◽

Nonvalvular Atrial Fibrillation ◽

Real World Evidence

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SIERRA-AMD: A Retrospective, Real-World Evidence Study of Patients with Neovascular Age-Related Macular Degeneration in the United States

Ophthalmology Retina ◽

10.1016/j.oret.2019.09.009 ◽

2020 ◽

Vol 4 (2) ◽

pp. 122-133 ◽

Cited By ~ 2

Author(s):

Arshad M. Khanani ◽

Adrian Skelly ◽

Vladimir Bezlyak ◽

Ray Griner ◽

Laura Rodriguez Torres ◽

...

Keyword(s):

United States ◽

Macular Degeneration ◽

Real World ◽

The United States ◽

Age Related Macular Degeneration ◽

Age Related ◽

Real World Evidence

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Systematic Literature Review of Real-World Evidence on Persistence, Switching, and Dose Escalation with Biologics in Inflammatory Bowel Disease in the United States

Value in Health ◽

10.1016/j.jval.2018.04.582 ◽

2018 ◽

Vol 21 ◽

pp. S87-S88

Author(s):

E Rupniewska ◽

D Singer ◽

S Khan ◽

M Neighbors ◽

JA Chiarappa ◽

...

Keyword(s):

United States ◽

Inflammatory Bowel Disease ◽

Literature Review ◽

Systematic Literature Review ◽

Dose Escalation ◽

Real World ◽

Bowel Disease ◽

The United States ◽

Real World Evidence ◽

Inflammatory Bowel

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Predictors and Outcomes of Hospitalization for Influenza: Real-World Evidence from the United States Medicare Population

Infectious Diseases and Therapy ◽

10.1007/s40121-020-00354-x ◽

2020 ◽

Author(s):

Susan C. Bolge ◽

Furaha Kariburyo ◽

Huseyin Yuce ◽

Roman Fleischhackl

Keyword(s):

United States ◽

Real World ◽

The United States ◽

Medicare Population ◽

Real World Evidence

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