EP.82A prospective study of eteplirsen treatment for Duchenne muscular dystrophy in routine clinical practice: study design and methodology

2019 ◽  
Vol 29 ◽  
pp. S176
Author(s):  
K. Tsai ◽  
R. Fischer ◽  
B. Chao ◽  
Y. Zheng ◽  
K. Moitoso ◽  
...  
Keyword(s):  
Clinical Practice ◽  
Duchenne Muscular Dystrophy ◽  
Muscular Dystrophy ◽  
Prospective Study ◽  
Study Design ◽  
Routine Clinical Practice ◽  
Practice Study

EP.71Behavioral problems in Duchenne muscular dystrophy: how do we manage them in clinical practice?

2019 ◽  
Vol 29 ◽  
pp. S173
Author(s):  
S. Geuens ◽  
M. Verly ◽  
J. Lemiere ◽  
N. Goemans ◽  
L. De Waele
Keyword(s):  
Clinical Practice ◽  
Duchenne Muscular Dystrophy ◽  
Muscular Dystrophy

scholarly journals Corrigendum to “Effectiveness and safety of perampanel as early add-on treatment in patients with epilepsy and focal seizures in the routine clinical practice: Spain prospective study (PERADON)” [Epilepsy Behav 102 (2020) 106655]

2020 ◽  
Vol 104 ◽  
pp. 106917
Author(s):  
Javier Abril Jaramillo ◽  
José Carlos Estévez María ◽  
Juan Miguel Girón Úbeda ◽  
Óscar Vega López ◽  
María Elena Calzado Rivas ◽  
...  
Keyword(s):  
Clinical Practice ◽  
Prospective Study ◽  
Routine Clinical Practice ◽  
Focal Seizures ◽  
Patients With Epilepsy

scholarly journals Effects of bisphosphonates on osteoporosis induced by Duchenne muscular dystrophy: A prospective study

Bone Reports ◽  
2020 ◽  
Vol 13 ◽  
pp. 100591
Author(s):  
Wenbin Zheng ◽  
Yi Dai ◽  
Jing Hu ◽  
Dichen Zhao ◽  
Ou Wang ◽  
...  
Keyword(s):  
Duchenne Muscular Dystrophy ◽  
Muscular Dystrophy ◽  
Prospective Study ◽  
A Prospective Study

scholarly journals High-dose biotin in progressive multiple sclerosis: A prospective study of 178 patients in routine clinical practice

2019 ◽  
Vol 26 (14) ◽  
pp. 1898-1906 ◽  
Author(s):  
Laura Couloume ◽  
Laetitia Barbin ◽  
Emmanuelle Leray ◽  
Sandrine Wiertlewski ◽  
Emmanuelle Le Page ◽  
...  
Keyword(s):  
Multiple Sclerosis ◽  
Clinical Practice ◽  
Prospective Study ◽  
Outcome Measures ◽  
Progressive Multiple Sclerosis ◽  
Routine Clinical Practice ◽  
High Dose ◽  
Disability Progression ◽  
Edss Score ◽  
Multiple Sclerosis Patients

Background: A recent controlled trial suggested that high-dose biotin supplementation reverses disability progression in patients with progressive multiple sclerosis. Objective: To analyze the impact of high-dose biotin in routine clinical practice on disability progression at 12 months. Methods: Progressive multiple sclerosis patients who started high-dose biotin at Nantes or Rennes Hospital between 3 June 2015 and 15 September 2017 were included in this prospective study. Disability outcome measures, patient-reported outcome measures, relapses, magnetic resonance imaging (MRI) data, and adverse events were collected at baseline, 6, and 12 months. Results: A total of 178 patients were included. At baseline, patients were 52.0 ± 9.4 years old, mean Expanded Disability Status Scale (EDSS) score was 6.1 ± 1.3, mean disease duration was 16.9 ± 9.5 years. At 12 months, 3.8% of the patients had an improved EDSS score. Regarding the other disability scales, scores either remained stable or increased significantly. In total, 47.4% of the patients described stability, 27.6% felt an improvement, and 25% described a worsening. Four patients (2.2%) had a relapse. Of the 74 patients (41.6%) who underwent an MRI, 20 (27.0%) had new T2 lesions, 8 (10.8%) had gadolinium-enhancing lesions. Twenty-five (14%) reported adverse event. Conclusion: In this study, high-dose biotin did not seem to be associated with a clear improvement in disability.

A multicentre prospective study on pemetrexed in the second line chemotherapy of non small cell lung cancer. Data from routine clinical practice

Lung Cancer ◽  
2012 ◽  
Vol 77 ◽  
pp. S33
Author(s):  
Vítězslav Kolek ◽  
Miloš Pešek ◽  
Ivona Grygárková ◽  
Petr Zatloukal ◽  
Jana Skřičková ◽  
...  
Keyword(s):  
Lung Cancer ◽  
Clinical Practice ◽  
Prospective Study ◽  
Small Cell ◽  
Routine Clinical Practice ◽  
Second Line ◽  
Small Cell Lung ◽  
Cancer Data ◽  
Multicentre Prospective Study ◽  
Line Chemotherapy

Treatment satisfaction in patients with rrms treated with teriflunomide in routine clinical practice: aubpro study design

2017 ◽  
Vol 88 (5) ◽  
pp. e1.45-e1
Author(s):  
Steve Vucic ◽  
Michael H Barnett ◽  
Stefan Blum ◽  
Neil Shuey ◽  
Richard Worrell ◽  
...  
Keyword(s):  
Clinical Practice ◽  
Study Design ◽  
Treatment Satisfaction ◽  
Routine Clinical Practice

Ampa study (a mirroring clinical practice study of perampanel in adults and adolescents) design: Real-world prospective study of perampanel as add-on therapy for focal-onset seizures

2021 ◽  
Vol 429 ◽  
pp. 119205
Author(s):  
Alfredo D’Aniello ◽  
Anna Teresa Giallonardo ◽  
Oriano Mecarelli ◽  
Umberto Aguglia ◽  
Giovanni Assenza ◽  
...  
Keyword(s):  
Clinical Practice ◽  
Prospective Study ◽  
Real World ◽  
Practice Study
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