scholarly journals Enzyme replacement in the CSF to treat metachromatic leukodystrophy in mouse model using single intracerebroventricular injection of self-complementary AAV1 vector

2015 ◽  
Vol 5 (1) ◽  
Author(s):  
Kohei Hironaka ◽  
Yoshiyuki Yamazaki ◽  
Yukihiko Hirai ◽  
Motoko Yamamoto ◽  
Noriko Miyake ◽  
...  
Keyword(s):  
Mouse Model ◽  
Metachromatic Leukodystrophy ◽  
Intracerebroventricular Injection ◽  
Enzyme Replacement ◽  
Aav1 Vector

scholarly journals Enzyme replacement improves nervous system pathology and function in a mouse model for metachromatic leukodystrophy

2005 ◽  
Vol 14 (9) ◽  
pp. 1139-1152 ◽  
Author(s):  
Ulrich Matzner ◽  
Eva Herbst ◽  
Kerstin Khalaj Hedayati ◽  
Renate Lüllmann-Rauch ◽  
Carsten Wessig ◽  
...  
Keyword(s):  
Nervous System ◽  
Mouse Model ◽  
Metachromatic Leukodystrophy ◽  
Enzyme Replacement ◽  
And Function

scholarly journals Enzyme Replacement Improves Ataxic Gait and Central Nervous System Histopathology in a Mouse Model of Metachromatic Leukodystrophy

2009 ◽  
Vol 17 (4) ◽  
pp. 600-606 ◽  
Author(s):  
Ulrich Matzner ◽  
Renate Lüllmann-Rauch ◽  
Stijn Stroobants ◽  
Claes Andersson ◽  
Cecilia Weigelt ◽  
...  
Keyword(s):  
Central Nervous System ◽  
Nervous System ◽  
Mouse Model ◽  
Metachromatic Leukodystrophy ◽  
Ataxic Gait ◽  
Enzyme Replacement

scholarly journals Efficacy of enzyme replacement therapy in an aggravated mouse model of metachromatic leukodystrophy declines with age

2012 ◽  
Vol 21 (11) ◽  
pp. 2599-2609 ◽  
Author(s):  
F. Matthes ◽  
S. Stroobants ◽  
D. Gerlach ◽  
C. Wohlenberg ◽  
C. Wessig ◽  
...  
Keyword(s):  
Mouse Model ◽  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Metachromatic Leukodystrophy ◽  
Enzyme Replacement

scholarly journals 218. Gene Therapy and Enzyme Replacement in a Mouse Model of Late Infantile Neuronal Ceroid Lipofuscinosis

2006 ◽  
Vol 13 ◽  
pp. S84
Author(s):  
Michael Chang ◽  
David Sleat ◽  
Seng Cheng ◽  
Marco Passini ◽  
Peter Lobel ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Mouse Model ◽  
Neuronal Ceroid Lipofuscinosis ◽  
Infantile Neuronal Ceroid Lipofuscinosis ◽  
Enzyme Replacement ◽  
Ceroid Lipofuscinosis

scholarly journals AAV1 Mediated Co-expression of Formylglycine-Generating Enzyme and Arylsulfatase A Efficiently Corrects Sulfatide Storage in a Mouse Model of Metachromatic Leukodystrophy

2007 ◽  
Vol 15 (1) ◽  
pp. 38-43 ◽  
Author(s):  
Toshiyuki Kurai ◽  
Sanae Hisayasu ◽  
Ryo Kitagawa ◽  
Makoto Migita ◽  
Hidenori Suzuki ◽  
...  
Keyword(s):  
Mouse Model ◽  
Metachromatic Leukodystrophy ◽  
Arylsulfatase A

Progressive neuropathology in the spinal cord of a mouse model of CLN1 disease and assessing the efficacy of intrathecal enzyme replacement therapy (ERT)

2016 ◽  
Vol 117 (2) ◽  
pp. S36 ◽  
Author(s):  
Jonathan Cooper ◽  
Jasmin Dmytrus ◽  
Sarmi Sri ◽  
Joshua Dearborn ◽  
Mark Sands ◽  
...  
Keyword(s):  
Spinal Cord ◽  
Mouse Model ◽  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Enzyme Replacement

Enzyme replacement therapy in a mouse model of aspartylglycosaminuria

2000 ◽  
Vol 14 (2) ◽  
pp. 361-367 ◽  
Author(s):  
Ulla Dunder ◽  
Vesa Kaartinen ◽  
Pirjo Valtonen ◽  
Eira VÄÄnÄnen ◽  
Veli-Matti Kosma ◽  
...  
Keyword(s):  
Mouse Model ◽  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Enzyme Replacement

Fetal Metachromatic Leukodystrophy: Pathology, Biochemistry and a Study of In Vitro Enzyme Replacement in CNS Tissue

1976 ◽  
Vol 35 (6) ◽  
pp. 622-632 ◽  
Author(s):  
S. E. Poduslo ◽  
G. Tennekoon ◽  
D. Price ◽  
K. Miller ◽  
G. M. McKhann
Keyword(s):  
Metachromatic Leukodystrophy ◽  
Enzyme Replacement
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