scholarly journals Hypotrichosis and juvenile macular dystrophy caused by CDH3 mutation: A candidate disease for retinal gene therapy

2016 ◽  
Vol 6 (1) ◽  
Author(s):  
Mandeep S. Singh ◽  
Suzanne Broadgate ◽  
Ranjana Mathur ◽  
Richard Holt ◽  
Stephanie Halford ◽  
...  
2018 ◽  
Vol 102 ◽  
pp. 136
Author(s):  
Alejandra Bosco ◽  
Sarah Anderson ◽  
Kevin Breen ◽  
Cesar Romero ◽  
Michael Steele ◽  
...  

2008 ◽  
Vol 360 (1-2) ◽  
pp. 177-183 ◽  
Author(s):  
A. del Pozo-Rodríguez ◽  
D. Delgado ◽  
M.A. Solinís ◽  
A.R. Gascón ◽  
J.L. Pedraz

2010 ◽  
Vol 29 (5) ◽  
pp. 376-397 ◽  
Author(s):  
Shannon M. Conley ◽  
Muna I. Naash

2017 ◽  
Vol 6 (4) ◽  
pp. 4 ◽  
Author(s):  
Anna P. Salvetti ◽  
Maria I. Patrício ◽  
Alun R. Barnard ◽  
Harry O. Orlans ◽  
Doron G. Hickey ◽  
...  

2020 ◽  
pp. 487-515
Author(s):  
Mark M. Hassall ◽  
Matthew P. Simunovic

2013 ◽  
Vol 83 (2) ◽  
pp. 131-140 ◽  
Author(s):  
G. Puras ◽  
J. Zarate ◽  
M. Aceves ◽  
A. Murua ◽  
A.R. Díaz ◽  
...  

Gene Therapy ◽  
2013 ◽  
Vol 20 (8) ◽  
pp. 824-833 ◽  
Author(s):  
V S Lopes ◽  
S E Boye ◽  
C M Louie ◽  
S Boye ◽  
F Dyka ◽  
...  

2020 ◽  
Vol 17 ◽  
pp. 505-519
Author(s):  
Elmar Carlos Hulliger ◽  
Simon Manuel Hostettler ◽  
Sonja Kleinlogel

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