Exonic Sequences Provide Better Targets for Antisense Oligonucleotides Than Splice Site Sequences in the Modulation of Duchenne Muscular Dystrophy Splicing

2010 ◽  
Vol 20 (2) ◽  
pp. 69-77 ◽  
Author(s):  
Annemieke Aartsma-Rus ◽  
Hellen Houlleberghs ◽  
Judith C.T. van Deutekom ◽  
Gert-Jan B. van Ommen ◽  
Peter A.C. 't Hoen
Keyword(s):  
Duchenne Muscular Dystrophy ◽  
Muscular Dystrophy ◽  
Splice Site ◽  
Antisense Oligonucleotides

In vivocomparison of 2′-O-methyl phosphorothioate and morpholino antisense oligonucleotides for Duchenne muscular dystrophy exon skipping

2009 ◽  
Vol 11 (3) ◽  
pp. 257-266 ◽  
Author(s):  
Hans A. Heemskerk ◽  
Christa L. de Winter ◽  
Sjef J. de Kimpe ◽  
Petra van Kuik-Romeijn ◽  
Niki Heuvelmans ◽  
...  
Keyword(s):  
Duchenne Muscular Dystrophy ◽  
Muscular Dystrophy ◽  
Antisense Oligonucleotides ◽  
Exon Skipping

scholarly journals Novel Cationic Carotenoid Lipids as Delivery Vectors of Antisense Oligonucleotides for Exon Skipping in Duchenne Muscular Dystrophy

Molecules ◽  
2012 ◽  
Vol 17 (2) ◽  
pp. 1138-1148 ◽  
Author(s):  
Linda J. Popplewell ◽  
Aseel Abu-Dayya ◽  
Tushar Khanna ◽  
Marcella Flinterman ◽  
Nada Abdul Khalique ◽  
...  
Keyword(s):  
Duchenne Muscular Dystrophy ◽  
Muscular Dystrophy ◽  
Antisense Oligonucleotides ◽  
Exon Skipping

T.P.1 04 Towards safe and efficient full-body delivery of antisense oligonucleotides for the treatment of Duchenne muscular dystrophy

2006 ◽  
Vol 16 (9-10) ◽  
pp. 685-686
Author(s):  
J.A. Heemskerk ◽  
C.L. de Winter ◽  
N. Heuvelmans ◽  
P. van Kuik ◽  
S. de Kimpe ◽  
...  
Keyword(s):  
Duchenne Muscular Dystrophy ◽  
Muscular Dystrophy ◽  
Antisense Oligonucleotides ◽  
Full Body
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