scholarly journals Long-term restoration of alpha-L-iduronidase activity in fibroblasts from patients with mucopolysaccharidosis type I after non-viral gene transfer

2017 ◽  
Vol 37 (4) ◽  
pp. 330-333
Author(s):  
Fabiano de Oliveira Poswar ◽  
Fabiana Quoos Mayer ◽  
Maira Burin ◽  
Ursula da Silveira Matte ◽  
Roberto Giugliani ◽  
...  
1993 ◽  
Vol 16 (6) ◽  
pp. 1024-1033 ◽  
Author(s):  
J. J. Hopwood ◽  
A. Vellodi ◽  
H. S. Scott ◽  
C. P. Morris ◽  
T. Litjens ◽  
...  

2006 ◽  
Vol 1076 (1) ◽  
pp. 225-230 ◽  
Author(s):  
Gustavo Kellermann Reolon ◽  
Luisa Macedo Braga ◽  
Melissa Camassola ◽  
Tatiana Luft ◽  
João Antônio Pêgas Henriques ◽  
...  

Sign in / Sign up

Export Citation Format

Share Document