The future for treatment by bone marrow transplantation for adrenoleukodystrophy, metachromatic leukodystrophy, globoid cell leukodystrophy and Hurler syndrome

Marrow Transplantation ◽

Metachromatic Leukodystrophy ◽

Hurler Syndrome ◽

The Future ◽

Bone marrow transplantation for globoid cell leukodystrophy, adrenoleukodystrophy, metachromatic leukodystrophy, and Hurler syndrome

Current Opinion in Hematology ◽

10.1097/00062752-199911000-00004 ◽

1999 ◽

Vol 6 (6) ◽

pp. 377 ◽

Cited By ~ 95

Author(s):

William Krivit ◽

Patrick Aubourg ◽

Elsa Shapiro ◽

Charles Peters

Keyword(s):

Bone Marrow ◽

Marrow Transplantation ◽

Metachromatic Leukodystrophy ◽

Hurler Syndrome ◽

Bone Marrow Transplantation Alters the Tremor Phenotype in the Murine Model of Globoid-Cell Leukodystrophy

Journal of Clinical Medicine ◽

10.3390/jcm1010001 ◽

2012 ◽

Vol 1 (1) ◽

pp. 1-14 ◽

Cited By ~ 14

Author(s):

Adarsh S. Reddy ◽

David F. Wozniak ◽

Nuri B. Farber ◽

Joshua T. Dearborn ◽

Stephen C. Fowler ◽

...

Keyword(s):

Bone Marrow ◽

Murine Model ◽

Marrow Transplantation ◽

Bone marrow transplantation increases efficacy of central nervous system-directed enzyme replacement therapy in the murine model of globoid cell leukodystrophy

Molecular Genetics and Metabolism ◽

10.1016/j.ymgme.2012.05.021 ◽

2012 ◽

Vol 107 (1-2) ◽

pp. 186-196 ◽

Cited By ~ 29

Author(s):

Elizabeth Y. Qin ◽

Jacqueline A. Hawkins-Salsbury ◽

Xuntian Jiang ◽

Adarsh S. Reddy ◽

Nuri B. Farber ◽

...

Keyword(s):

Central Nervous System ◽

Bone Marrow ◽

Nervous System ◽

Enzyme Replacement Therapy ◽

Murine Model ◽

Marrow Transplantation ◽

Enzyme Replacement ◽

Central Nervous System-directed AAV2/5-Mediated Gene Therapy Synergizes with Bone Marrow Transplantation in the Murine Model of Globoid-cell Leukodystrophy

Molecular Therapy ◽

10.1038/sj.mt.6300026 ◽

2007 ◽

Vol 15 (1) ◽

pp. 44-52 ◽

Cited By ~ 52

Author(s):

Darshong Lin ◽

Anthony Donsante ◽

Shannon Macauley ◽

Beth Levy ◽

Carole Vogler ◽

...

Keyword(s):

Gene Therapy ◽

Central Nervous System ◽

Bone Marrow ◽

Nervous System ◽

Murine Model ◽

Marrow Transplantation ◽

Bone Marrow Transplantation Augments the Effect of Brain- and Spinal Cord-Directed Adeno-Associated Virus 2/5 Gene Therapy by Altering Inflammation in the Murine Model of Globoid-Cell Leukodystrophy

Journal of Neuroscience ◽

10.1523/jneurosci.1802-11.2011 ◽

2011 ◽

Vol 31 (27) ◽

pp. 9945-9957 ◽

Cited By ~ 44

Author(s):

A. S. Reddy ◽

J. H. Kim ◽

J. A. Hawkins-Salsbury ◽

S. L. Macauley ◽

E. T. Tracy ◽

...

Keyword(s):

Spinal Cord ◽

Gene Therapy ◽

Bone Marrow ◽

Murine Model ◽

Marrow Transplantation ◽

Adeno Associated Virus ◽

Brain And Spinal Cord ◽

424. Intracranial AAV5 Synergizes with Non-Myeloablative Bone Marrow Transplantation in the Murine Model of Globoid-Cell Leukodystrophy

Molecular Therapy ◽

10.1016/j.ymthe.2005.06.426 ◽

2005 ◽

Vol 11 ◽

pp. S164-S165

Keyword(s):

Bone Marrow ◽

Murine Model ◽

Marrow Transplantation ◽

IL-6 deficiency allows for enhanced therapeutic value after bone marrow transplantation across a minor histocompatibility barrier in the twitcher (globoid cell leukodystrophy) mouse

Journal of Neuroscience Research ◽

10.1002/jnr.1154 ◽

2001 ◽

Vol 65 (4) ◽

pp. 298-307 ◽

Cited By ~ 4

Author(s):

Sangita Biswas ◽

David M. Pinson ◽

Illya G. Bronshteyn ◽

Steven M. LeVine

Keyword(s):

Bone Marrow ◽

Marrow Transplantation ◽

Therapeutic Value ◽

A Minor ◽

Neurological Improvement Following Bone Marrow Transplantation in Twitcher Mice — Murine Globoid Cell Leukodystrophy

Lipid Storage Disorders ◽

10.1007/978-1-4613-1029-7_99 ◽

1988 ◽

pp. 785-790

Author(s):

Peter M. Hoogerbrugge ◽

Ben J. H. M. Poorthuis ◽

Takuro Kobayashi ◽

Gerard Wagemaker ◽

Kinuko Suzuki

Keyword(s):

Bone Marrow ◽

Marrow Transplantation ◽

Neurological Improvement ◽

Allogeneic bone marrow transplantation for infantile globoid-cell leukodystrophy (Krabbe's disease)

Pediatric Transplantation ◽

10.1034/j.1399-3046.2002.02026.x ◽

2002 ◽

Vol 6 (5) ◽

pp. 427-431 ◽

Cited By ~ 19

Author(s):

Maurizio Caniglia ◽

Ippolita Rana ◽

Rita Maria Pinto ◽

Giuseppe Fariello ◽

Roberta Caruso ◽

...

Keyword(s):

Bone Marrow ◽

Marrow Transplantation ◽

Allogeneic Bone Marrow Transplantation ◽

Allogeneic Bone Marrow ◽

Allogeneic Bone ◽

Krabbe's Disease ◽

Krabbe’S Disease ◽

Substrate-Reduction Therapy Enhances the Benefits of Bone Marrow Transplantation in Young Mice with Globoid Cell Leukodystrophy

Pediatric Research ◽

10.1203/00006450-200201000-00009 ◽

2002 ◽

Vol 51 (1) ◽

pp. 40-47 ◽

Cited By ~ 42

Author(s):

Sangita Biswas ◽

Steven M Le Vine

Keyword(s):

Bone Marrow ◽

Marrow Transplantation ◽

Substrate Reduction Therapy ◽

Substrate Reduction ◽

Globoid Cell ◽

Young Mice