Caregiver Preferences for Emerging Duchenne Muscular Dystrophy Treatments: A Comparison of Best-Worst Scaling and Conjoint Analysis

The Patient: Patient-Centered Outcomes Research ◽

10.1007/s40271-014-0104-x ◽

2014 ◽

Vol 8 (1) ◽

pp. 19-27 ◽

Author(s):

Ilene L. Hollin ◽

Holly L. Peay ◽

John F. P. Bridges

Keyword(s):

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy ◽

Conjoint Analysis ◽

Best Worst Scaling

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Prioritizing Parental Worry Associated with Duchenne Muscular Dystrophy Using Best-Worst Scaling

Journal of Genetic Counseling ◽

10.1007/s10897-015-9872-2 ◽

2015 ◽

Vol 25 (2) ◽

pp. 305-313 ◽

Author(s):

Holly Landrum Peay ◽

I. L. Hollin ◽

J. F. P. Bridges

Keyword(s):

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy ◽

Best Worst Scaling

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P.2.20 Prioritizing the worries of parents of children with Duchenne muscular dystrophy using best-worst scaling

Neuromuscular Disorders ◽

10.1016/j.nmd.2013.06.425 ◽

2013 ◽

Vol 23 (9-10) ◽

pp. 755 ◽

Author(s):

H. Peay

Keyword(s):

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy ◽

Best Worst Scaling

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Priorities when deciding on participation in early-phase gene therapy trials for Duchenne muscular dystrophy: a best–worst scaling experiment in caregivers and adult patients

Orphanet Journal of Rare Diseases ◽

10.1186/s13023-019-1069-6 ◽

2019 ◽

Vol 14 (1) ◽

Author(s):

Ryan S. Paquin ◽

Ryan Fischer ◽

Carol Mansfield ◽

Brennan Mange ◽

Katherine Beaverson ◽

...

Keyword(s):

Gene Therapy ◽

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy ◽

Early Phase ◽

Adult Patients ◽

Best Worst Scaling

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Measurement of respiratory function decline in patients with Duchenne muscular dystrophy: a conjoint analysis

Neurodegenerative Disease Management ◽

10.2217/nmt-2017-0052 ◽

2018 ◽

Vol 8 (2) ◽

pp. 89-96 ◽

Author(s):

Elena Ripamonti ◽

Grazia D'Angelo

Keyword(s):

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy ◽

Conjoint Analysis ◽

Respiratory Function

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Impact of Bisphosphonates on Survival for Patients With Duchenne Muscular Dystrophy

Yearbook of Neurology and Neurosurgery ◽

10.1016/j.yneu.2011.04.066 ◽

2011 ◽

Vol 2011 ◽

pp. 198-199

Author(s):

G.N. Breningstall

Keyword(s):

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy

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Treatment of Duchenne muscular dystrophy with cyclosporin A – A randomized, double-blind, placebo controlled trial

Neuropediatrics ◽

10.1055/s-0029-1215757 ◽

2008 ◽

Vol 39 (05) ◽

Author(s):

J Kirschner ◽

J Schessl ◽

G Ihorst ◽

R Korinthenberg

Keyword(s):

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy ◽

Cyclosporin A ◽

Controlled Trial ◽

Double Blind ◽

Double Blind Placebo

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Health- related quality of life in patients with Duchenne Muscular Dystrophy

Neuropediatrics ◽

10.1055/s-0031-1273950 ◽

2011 ◽

Vol 42 (S 01) ◽

Author(s):

B Geers ◽

S Elsenbruch ◽

J Schmid ◽

U Schara

Keyword(s):

Quality Of Life ◽

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy ◽

Health Related Quality ◽

Related Quality ◽

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Integrating pediatric palliative care across the spectrum of life threatening pediatric neuromuscular disorders focused on Spinal muscular atrophy type I and Duchenne muscular dystrophy

Neuropediatrics ◽

10.1055/s-0031-1274094 ◽

2011 ◽

Vol 42 (S 01) ◽

Author(s):

M von der Hagen ◽

M Smitka ◽

A Pyper ◽

M Breiting ◽

A Müller ◽

...

Keyword(s):

Palliative Care ◽

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy ◽

Spinal Muscular Atrophy ◽

Muscular Atrophy ◽

Neuromuscular Disorders ◽

Pediatric Palliative Care ◽

Type I ◽

Spinal Muscular Atrophy Type ◽

Life Threatening

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Growth and psychomotor development of patients with Duchenne Muscular Dystrophy

Neuropediatrics ◽

10.1055/s-0032-1307138 ◽

2012 ◽

Vol 43 (02) ◽

Author(s):

E Sarrazin ◽

M von der Hagen ◽

U Schara ◽

K von Au ◽

A Kaindl

Keyword(s):

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy ◽

Psychomotor Development

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Current care practice in Duchenne muscular dystrophy in Europe - results of the CARE-NMD cross-sectional survey

Neuropediatrics ◽

10.1055/s-0033-1337747 ◽

2013 ◽

Vol 44 (02) ◽

Author(s):

J Vry ◽

K Gramsch ◽

K Bushby ◽

H Lochmüller ◽

S Rodger ◽

...

Keyword(s):

Duchenne Muscular Dystrophy ◽

Muscular Dystrophy ◽

Care Practice ◽

Cross Sectional Survey ◽

Cross Sectional

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