Hematopoietic stem cell gene editing and expansion: state-of-the-art technologies and recent applications

2021 ◽  
Author(s):  
Myriam L.R. Haltalli ◽  
Adam C. Wilkinson ◽  
Alejo Rodriguez-Fraticelli ◽  
Matthew Porteus
Keyword(s):  
Stem Cell ◽  
Hematopoietic Stem Cell ◽  
Gene Editing ◽  
State Of The Art ◽  
Hematopoietic Stem ◽  
Cell Gene ◽  
Stem Cell Gene

Hematopoietic stem cell gene therapy: The optimal use of lentivirus and gene editing approaches

Blood Reviews ◽  
2020 ◽  
Vol 40 ◽  
pp. 100641 ◽  
Author(s):  
Andrés Lamsfus-Calle ◽  
Alberto Daniel-Moreno ◽  
Guillermo Ureña-Bailén ◽  
Janani Raju ◽  
Justin S. Antony ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Hematopoietic Stem Cell ◽  
Gene Editing ◽  
Hematopoietic Stem ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy

scholarly journals Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper‐IgM syndrome

2021 ◽  
Author(s):  
Valentina Vavassori ◽  
Elisabetta Mercuri ◽  
Genni E Marcovecchio ◽  
Maria C Castiello ◽  
Giulia Schiroli ◽  
...  
Keyword(s):  
Stem Cell ◽  
T Cell ◽  
Hematopoietic Stem Cell ◽  
Gene Editing ◽  
Comparable Efficacy ◽  
Hematopoietic Stem ◽  
Hyper Igm Syndrome ◽  
Hyper Igm ◽  
Cell Gene ◽  
Stem Cell Gene

scholarly journals 37. Towards Clinical Translation of Hematopoietic Stem Cell Gene Editing for the Correction of SCID-X1 Mutations

2016 ◽  
Vol 24 ◽  
pp. S16-S17
Author(s):  
Pietro Genovese ◽  
Giulia Schiroli ◽  
Anthony Conway ◽  
Samuele Ferrari ◽  
Dmitry Y. Guschin ◽  
...  
Keyword(s):  
Stem Cell ◽  
Hematopoietic Stem Cell ◽  
Gene Editing ◽  
Clinical Translation ◽  
Hematopoietic Stem ◽  
Cell Gene ◽  
Stem Cell Gene

Preclinical modeling highlights the therapeutic potential of hematopoietic stem cell gene editing for correction of SCID-X1

2017 ◽  
Vol 9 (411) ◽  
pp. eaan0820 ◽  
Author(s):  
Giulia Schiroli ◽  
Samuele Ferrari ◽  
Anthony Conway ◽  
Aurelien Jacob ◽  
Valentina Capo ◽  
...  
Keyword(s):  
Stem Cell ◽  
Hematopoietic Stem Cell ◽  
Gene Editing ◽  
Therapeutic Potential ◽  
Hematopoietic Stem ◽  
Cell Gene ◽  
Stem Cell Gene

Long-term hematopoietic stem cell gene therapy corrects neuromuscular manifestations in preclinical study of Pompe mice

2021 ◽  
Vol 132 (2) ◽  
pp. S107
Author(s):  
Niek P. van Til ◽  
Yildirim Dogan ◽  
Cecilia Barese ◽  
Zeenath Unnisa ◽  
Swaroopa Guda ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Hematopoietic Stem Cell ◽  
Preclinical Study ◽  
Hematopoietic Stem ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy
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