216. Gene Therapy of Huntington Disease Using RNA Interference and Sleeping Beauty Transposon

Gene Therapy of Huntington Disease Using RNA Interference and Sleeping Beauty Transposon

Molecular Therapy ◽

10.1016/s1525-0016(04)00444-7 ◽

2004 ◽

Keyword(s):

Gene Therapy ◽

Rna Interference ◽

Huntington Disease ◽

Sleeping Beauty ◽

Sleeping Beauty Transposon

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Cell-Based Gene Therapy Using the Sleeping Beauty Transposon System Reduces Neovascularisation in Rats

SSRN Electronic Journal ◽

10.2139/ssrn.3408024 ◽

2019 ◽

Author(s):

Maria Hernandez ◽

Sergio Recalde ◽

Laura Garcia-Garcia ◽

Jaione Bezunartea ◽

Csaba Miskey ◽

...

Keyword(s):

Gene Therapy ◽

Sleeping Beauty ◽

Sleeping Beauty Transposon

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728. A Liver-Specific Promoter Enhances Expression of alpha-L-Iduronidase in Sleeping Beauty Transposon-Mediated Gene Therapy of Murine MPS I

Molecular Therapy ◽

10.1016/s1525-0016(16)38169-2 ◽

2010 ◽

Vol 18 ◽

pp. S284 ◽

Cited By ~ 1

Keyword(s):

Gene Therapy ◽

Sleeping Beauty ◽

Sleeping Beauty Transposon ◽

Mps I

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High and long-term von Willebrand factor expression after Sleeping Beauty transposon-mediated gene therapy in a mouse model of severe von Willebrand disease

Journal of Thrombosis and Haemostasis ◽

10.1111/jth.13938 ◽

2018 ◽

Vol 16 (3) ◽

pp. 592-604 ◽

Cited By ~ 9

Author(s):

I. Portier ◽

K. Vanhoorelbeke ◽

S. Verhenne ◽

I. Pareyn ◽

N. Vandeputte ◽

...

Keyword(s):

Gene Therapy ◽

Mouse Model ◽

Von Willebrand Factor ◽

Sleeping Beauty ◽

Von Willebrand Disease ◽

Sleeping Beauty Transposon ◽

Factor Expression ◽

Von Willebrand ◽

Willebrand Factor

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Gene Therapy with the Sleeping Beauty Transposon System

Trends in Genetics ◽

10.1016/j.tig.2017.08.008 ◽

2017 ◽

Vol 33 (11) ◽

pp. 852-870 ◽

Cited By ~ 41

Author(s):

Partow Kebriaei ◽

Zsuzsanna Izsvák ◽

Suneel A. Narayanavari ◽

Harjeet Singh ◽

Zoltán Ivics

Keyword(s):

Gene Therapy ◽

Sleeping Beauty ◽

Sleeping Beauty Transposon

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Long-Term Prevention of Congenital Thrombotic Thrombocytopenic Purpura in ADAMTS13 Knockout Mice by Sleeping Beauty Transposon-Mediated Gene Therapy

Arteriosclerosis Thrombosis and Vascular Biology ◽

10.1161/atvbaha.116.308680 ◽

2017 ◽

Vol 37 (5) ◽

pp. 836-844 ◽

Cited By ~ 10

Author(s):

Sebastien Verhenne ◽

Nele Vandeputte ◽

Inge Pareyn ◽

Zsuzsanna Izsvák ◽

Hanspeter Rottensteiner ◽

...

Keyword(s):

Gene Therapy ◽

Thrombotic Thrombocytopenic Purpura ◽

Knockout Mice ◽

Sleeping Beauty ◽

Thrombocytopenic Purpura ◽

Sleeping Beauty Transposon ◽

Congenital Thrombotic Thrombocytopenic Purpura

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447. Quantification of Alpha-L-Iduronidase Expression Outcomes in Mice Following Sleeping Beauty Transposon-Mediated Gene Therapy

Molecular Therapy ◽

10.1016/s1525-0016(16)34782-7 ◽

2013 ◽

Vol 21 ◽

pp. S172-S173

Keyword(s):

Gene Therapy ◽

Sleeping Beauty ◽

Sleeping Beauty Transposon

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Sleeping Beauty Transposon System is a Reliable Gene Delivery Tool for Hereditary Tyrosinaemia Type 1 Disease Gene Therapy: Size of the Foreign Gene Decides the Timing of Stable Integration into the Host Chromosomes

Journal of International Medical Research ◽

10.1177/030006051204000523 ◽

2012 ◽

Vol 40 (5) ◽

pp. 1850-1859 ◽

Cited By ~ 6

Author(s):

X-J Pan ◽

Z-Z Ma ◽

Q-J Zhang ◽

L Fan ◽

Q-H Li

Keyword(s):

Gene Therapy ◽

Gene Delivery ◽

Disease Gene ◽

Sleeping Beauty ◽

Foreign Gene ◽

Tyrosinaemia Type ◽

Sleeping Beauty Transposon ◽

Stable Integration ◽

Tyrosinaemia Type 1

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The Sleeping Beauty transposon system: a non-viral vector for gene therapy

Human Molecular Genetics ◽

10.1093/hmg/ddr140 ◽

2011 ◽

Vol 20 (R1) ◽

pp. R14-R20 ◽

Cited By ~ 93

Author(s):

E. L. Aronovich ◽

R. S. McIvor ◽

P. B. Hackett

Keyword(s):

Gene Therapy ◽

Viral Vector ◽

Sleeping Beauty ◽

Sleeping Beauty Transposon ◽

System A

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Sleeping Beauty Transposon-Mediated Nonviral Gene Therapy

BioDrugs ◽

10.2165/00063030-200620040-00003 ◽

2006 ◽

Vol 20 (4) ◽

pp. 219-229 ◽

Cited By ~ 12

Author(s):

Stephen Fernando ◽

Bradley S Fletcher

Keyword(s):

Gene Therapy ◽

Sleeping Beauty ◽

Nonviral Gene Therapy ◽

Sleeping Beauty Transposon

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