427. AAV2- and AAV5-Mediated CNS Delivery of Human CLN2 Reduces Lysosomal Storage in a Mouse Model of Late Infantile Neuronal Ceroid Lipofuscinosis
2012 ◽
Vol 107
(1-2)
◽
pp. 213-221
◽
Jie Hu
◽
Jui-Yun Lu
◽
Andrew M.S. Wong
◽
Linda S. Hynan
◽
Shari G. Birnbaum
◽
...
Michael Chang
◽
David Sleat
◽
Seng Cheng
◽
Marco Passini
◽
Peter Lobel
◽
...
2002 ◽
Vol 28
(2)
◽
pp. 158-159
◽
J. D. Cooper
◽
P. Gupta
◽
E. Bible
◽
S. Hofmann
◽
P. Lantos)
◽
...
2012 ◽
Vol 21
(10)
◽
pp. 2233-2244
◽
Arjun Saha
◽
Chinmoy Sarkar
◽
Satya P. Singh
◽
Zhongjian Zhang
◽
Jeeva Munasinghe
◽
...
2019 ◽
Vol 126
(2)
◽
pp. S63-S64
Steven J. Gray
◽
Alejandra Rozenberg
◽
Erik Lykken
◽
Linas Padegimas
◽
Timothy Miller
2007 ◽
Vol 8
(1)
◽
pp. 95
◽
Xingwen Qiao
◽
Jui-Yun Lu
◽
Sandra L Hofmann
2004 ◽
Vol 16
(2)
◽
pp. 346-359
◽
Ellen Bible
◽
Praveena Gupta
◽
Sandra L Hofmann
◽
Jonathan D Cooper
2014 ◽
Vol 25
(3)
◽
pp. 223-239
◽
Dolan Sondhi
◽
Emma C. Scott
◽
Alvin Chen
◽
Neil R. Hackett
◽
Andrew M.S. Wong
◽
...
2008 ◽
Vol 16
(4)
◽
pp. 649-656
◽
Michael Chang
◽
Jonathan D Cooper
◽
David E Sleat
◽
Seng H Cheng
◽
James C Dodge
◽
...
2018 ◽
Vol 123
(2)
◽
pp. S124
◽
Alejandra J. Rozenberg
◽
Erik Lykken
◽
Kaye Spratt
◽
Timothy J. Miller
◽
Steven J. Gray