Faculty Opinions recommendation of SIN retroviral vectors expressing COL7A1 under human promoters for ex vivo gene therapy of recessive dystrophic epidermolysis bullosa.

Ex Vivo Gene Therapy ◽

SIN Retroviral Vectors Expressing COL7A1 Under Human Promoters for Ex Vivo Gene Therapy of Recessive Dystrophic Epidermolysis Bullosa

Molecular Therapy ◽

10.1038/mt.2010.91 ◽

2010 ◽

Vol 18 (8) ◽

pp. 1509-1518 ◽

Cited By ~ 72

Author(s):

Matthias Titeux ◽

Valérie Pendaries ◽

Maria A Zanta-Boussif ◽

Audrey Décha ◽

Nathalie Pironon ◽

...

Keyword(s):

Gene Therapy ◽

Epidermolysis Bullosa ◽

Ex Vivo ◽

Retroviral Vectors ◽

Ex Vivo Gene Therapy ◽

Phase I/II Ex Vivo Gene Therapy Clinical Trial for Recessive Dystrophic Epidermolysis Bullosa Using Skin Equivalent Grafts Genetically Corrected with a COL7A1-Encoding SIN Retroviral Vector (GENEGRAFT)

Human Gene Therapy Clinical Development ◽

10.1089/humc.2014.2508 ◽

2014 ◽

Vol 25 (2) ◽

pp. 65-66 ◽

Cited By ~ 6

Keyword(s):

Clinical Trial ◽

Gene Therapy ◽

Phase I ◽

Epidermolysis Bullosa ◽

Ex Vivo ◽

Retroviral Vector ◽

Ex Vivo Gene Therapy ◽

Therapy Clinical Trial

Patient pre-selection outcomes for the European GENEGRAFT ex vivo phase I/II gene therapy trial for recessive dystrophic epidermolysis bullosa.

10.26226/morressier.595a9c56d462b80296c9fadf ◽

2017 ◽

Author(s):

Su Lwin

Keyword(s):

Gene Therapy ◽

Phase I ◽

Epidermolysis Bullosa ◽

Ex Vivo ◽

Gene Therapy Trial ◽

Therapy Trial

EBGene trial: patient preselection outcomes for the European GENEGRAFT ex vivo phase I/II gene therapy trial for recessive dystrophic epidermolysis bullosa

British Journal of Dermatology ◽

10.1111/bjd.18559 ◽

2019 ◽

Vol 182 (3) ◽

pp. 794-797 ◽

Cited By ~ 6

Author(s):

S. Gaucher ◽

S.M. Lwin ◽

M. Titeux ◽

A. Abdul‐Wahab ◽

N. Pironon ◽

...

Keyword(s):

Gene Therapy ◽

Phase I ◽

Epidermolysis Bullosa ◽

Ex Vivo ◽

Gene Therapy Trial ◽

Therapy Trial

227 Patient pre-selection outcomes for the European GENEGRAFT ex vivo phase I/II gene therapy trial for recessive dystrophic epidermolysis bullosa

Journal of Investigative Dermatology ◽

10.1016/j.jid.2017.07.224 ◽

2017 ◽

Vol 137 (10) ◽

pp. S231

Author(s):

S.M. Lwin ◽

S. Gaucher ◽

M. Titeux ◽

A. Abdul-Wahab ◽

N. Pironon ◽

...

Keyword(s):

Gene Therapy ◽

Phase I ◽

Epidermolysis Bullosa ◽

Ex Vivo ◽

Gene Therapy Trial ◽

Therapy Trial

Toward Epidermal Stem Cell-Mediated ex Vivo Gene Therapy of Junctional Epidermolysis Bullosa

Human Gene Therapy ◽

10.1089/104303400750035825 ◽

2000 ◽

Vol 11 (16) ◽

pp. 2283-2287 ◽

Cited By ~ 40

Author(s):

Elena Dellambra ◽

Graziella Pellegrini ◽

Liliana Guerra ◽

Giuliana Ferrari ◽

Giovanna Zambruno ◽

...

Keyword(s):

Gene Therapy ◽

Stem Cell ◽

Epidermolysis Bullosa ◽

Ex Vivo ◽

Epidermal Stem Cell ◽

Junctional Epidermolysis Bullosa ◽

Ex Vivo Gene Therapy

Gene therapy for recessive dystrophic epidermolysis bullosa

Chinese Journal of Dermatology ◽

10.35541/cjd.20210499 ◽

2021 ◽

Keyword(s):

Gene Therapy ◽

Epidermolysis Bullosa ◽

Targeted ex-vivo correction of COL7A1 through RNP-based CRISPR/Cas9 and Homology-Directed Repair to treat recessive dystrophic epidermolysis bullosa

10.26226/morressier.61081ff8bc981037240fe427 ◽

2021 ◽

Author(s):

Araksya Izmiryan

Keyword(s):

Epidermolysis Bullosa ◽

Ex Vivo ◽

Homology Directed Repair ◽

The potential of gene therapy for recessive dystrophic epidermolysis bullosa

British Journal of Dermatology ◽

10.1111/bjd.20910 ◽

2021 ◽

Author(s):

K.S. Subramaniam ◽

M.N. Antoniou ◽

J.A. McGrath ◽

S.M. Lwin

Keyword(s):

Gene Therapy ◽

Epidermolysis Bullosa ◽

The road to gene therapy for recessive dystrophic epidermolysis bullosa

Cell and Gene Therapy Insights ◽

10.18609/cgti.2017.011 ◽

2017 ◽

Vol 3 (2) ◽

pp. 75-81

Author(s):

Peter M Marinkovich ◽

Ngon T Nguyen ◽

Zurab Siprashvili

Keyword(s):

Gene Therapy ◽

Epidermolysis Bullosa ◽

The Road ◽