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Toward Epidermal Stem Cell-Mediated ex Vivo Gene Therapy of Junctional Epidermolysis Bullosa
Human Gene Therapy
◽
10.1089/104303400750035825
◽
2000
◽
Vol 11
(16)
◽
pp. 2283-2287
◽
Cited By ~ 40
Author(s):
Elena Dellambra
◽
Graziella Pellegrini
◽
Liliana Guerra
◽
Giuliana Ferrari
◽
Giovanna Zambruno
◽
...
Keyword(s):
Gene Therapy
◽
Stem Cell
◽
Epidermolysis Bullosa
◽
Ex Vivo
◽
Epidermal Stem Cell
◽
Junctional Epidermolysis Bullosa
◽
Ex Vivo Gene Therapy
Download Full-text
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10.15252/emmm.201404353
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Vol 7
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512 Stem cell sampling from the first trimester fetus for prenatal ex-vivo gene therapy: Feasibility study
American Journal of Obstetrics and Gynecology
◽
10.1016/s0002-9378(01)80544-5
◽
2001
◽
Vol 185
(6)
◽
pp. S221
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902. Mucopolysaccharidosis Type I Ex Vivo Gene Therapy Based on MLV-Mesenchymal Stem Cell Transduction: Is There a Way To Be Attenuated When Older?
Molecular Therapy
◽
10.1016/s1525-0016(16)39260-7
◽
2009
◽
Vol 17
◽
pp. S345
Keyword(s):
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◽
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SIN Retroviral Vectors Expressing COL7A1 Under Human Promoters for Ex Vivo Gene Therapy of Recessive Dystrophic Epidermolysis Bullosa
Molecular Therapy
◽
10.1038/mt.2010.91
◽
2010
◽
Vol 18
(8)
◽
pp. 1509-1518
◽
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Phase I/II Ex Vivo Gene Therapy Clinical Trial for Recessive Dystrophic Epidermolysis Bullosa Using Skin Equivalent Grafts Genetically Corrected with a COL7A1-Encoding SIN Retroviral Vector (GENEGRAFT)
Human Gene Therapy Clinical Development
◽
10.1089/humc.2014.2508
◽
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◽
Vol 25
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◽
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◽
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◽
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◽
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Retroviral Vector
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◽
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◽
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Generation of Human Induced Pluripotent Stem Cell-Derived Bona Fide Neural Stem Cells for Ex Vivo Gene Therapy of Metachromatic Leukodystrophy
Stem Cells Translational Medicine
◽
10.5966/sctm.2015-0414
◽
2016
◽
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◽
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◽
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Author(s):
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◽
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◽
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◽
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Ex vivo Gene Therapy for Epidermolysis Bullosa
New Technologies in Dermatological Science and Practice
◽
10.1201/9781003121275-14
◽
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◽
pp. 136-148
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◽
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◽
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Faculty Opinions recommendation of SIN retroviral vectors expressing COL7A1 under human promoters for ex vivo gene therapy of recessive dystrophic epidermolysis bullosa.
Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature
◽
10.3410/f.718345163.793493591
◽
2014
◽
Author(s):
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◽
Michael Vanden Oever
Keyword(s):
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Ultrasound-guided stem cell sampling from the early ovine fetus for prenatal ex vivo gene therapy
American Journal of Obstetrics and Gynecology
◽
10.1067/mob.2002.126982
◽
2002
◽
Vol 187
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◽
pp. 960-963
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Faculty Opinions recommendation of Sustained correction of X-linked severe combined immunodeficiency by ex vivo gene therapy.
Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature
◽
10.3410/f.1005837.70356
◽
2002
◽
Author(s):
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