Clinical Protocol: Phase I Clinical Trial Utilizing Gene Therapy for Limb Girdle Muscular Dystrophy: alpha-, beta-, gamma-, or delta-Sarcoglycan Gene Delivered with Intramuscular Instillations of Adeno-Associated Vectors

2000 ◽  
Vol 11 (5) ◽  
pp. 777-790 ◽  
1997 ◽  
Vol 20 (5) ◽  
pp. 400
Author(s):  
D. Kinzler ◽  
H. Tahara ◽  
E. Elder ◽  
C. Johnson ◽  
N. Nguyen ◽  
...  

1999 ◽  
Vol 10 (7) ◽  
pp. 1239-1250 ◽  
Author(s):  
James R. Herman ◽  
Howard L. Adler ◽  
Estuardo Aguilar-Cordova ◽  
Augusto Rojas-Martinez ◽  
Savio Woo ◽  
...  

2011 ◽  
Vol 70 (2) ◽  
pp. 207-212 ◽  
Author(s):  
David J. Fink ◽  
James Wechuck ◽  
Marina Mata ◽  
Joseph C. Glorioso ◽  
James Goss ◽  
...  

2013 ◽  
Author(s):  
Louis Buscail ◽  
Barbara Bournet ◽  
Fabienne Vernejoul ◽  
Hubert Lulka ◽  
Gilles Cambois ◽  
...  

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