Administration of a Replication-Deficient Adeno-Associated Virus Gene Transfer Vector Expressing the HumanCLN2cDNA to the Brain of Children with Late Infantile Neuronal Ceroid Lipofuscinosis

2004 ◽  
Vol 15 (11) ◽  
pp. 1131-1154 ◽  
Keyword(s):  
Gene Transfer ◽  
Neuronal Ceroid Lipofuscinosis ◽  
Adeno Associated Virus ◽  
Transfer Vector ◽  
Virus Gene ◽  
Infantile Neuronal Ceroid Lipofuscinosis ◽  
Ceroid Lipofuscinosis ◽  
Gene Transfer Vector ◽  
The Brain

Treatment of Late Infantile Neuronal Ceroid Lipofuscinosis by CNS Administration of a Serotype 2 Adeno-Associated Virus Expressing CLN2 cDNA

2008 ◽  
Vol 19 (5) ◽  
pp. 463-474 ◽  
Author(s):  
Stefan Worgall ◽  
Dolan Sondhi ◽  
Neil R. Hackett ◽  
Barry Kosofsky ◽  
Minal V. Kekatpure ◽  
...  
Keyword(s):  
Neuronal Ceroid Lipofuscinosis ◽  
Adeno Associated Virus ◽  
Infantile Neuronal Ceroid Lipofuscinosis ◽  
Ceroid Lipofuscinosis

MRI Evaluation of the Brain in Infantile Neuronal Ceroid-Lipofuscinosis

1995 ◽  
Vol 10 (6) ◽  
pp. 444-450 ◽  
Author(s):  
Sanna-Leena Vanhanen ◽  
Raili Raininko ◽  
Taina Autti ◽  
Pirkko Santavuori
Keyword(s):  
Neuronal Ceroid Lipofuscinosis ◽  
Infantile Neuronal Ceroid Lipofuscinosis ◽  
Ceroid Lipofuscinosis ◽  
The Brain ◽  
Mri Evaluation

scholarly journals Safety of Adeno-Associated Virus as Cochlear Gene Transfer Vector: Analysis of Distant Spread Beyond Injected Cochleae

2000 ◽  
Vol 2 (4) ◽  
pp. 368-373 ◽  
Author(s):  
Soochuen T. Kho ◽  
Robert M. Pettis ◽  
Anand N. Mhatre ◽  
Anil K. Lalwani
Keyword(s):  
Gene Transfer ◽  
Vector Analysis ◽  
Adeno Associated Virus ◽  
Transfer Vector ◽  
Gene Transfer Vector ◽  
Distant Spread

Hot Topics in Adeno-Associated Virus as a Gene Transfer Vector

2001 ◽  
Vol 19 (3) ◽  
pp. 229-238 ◽  
Author(s):  
Na Zhao ◽  
De-Pei Liu ◽  
Chih-Chuan Liang
Keyword(s):  
Gene Transfer ◽  
Adeno Associated Virus ◽  
Transfer Vector ◽  
Gene Transfer Vector
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