scholarly journals Gene therapy for Hurler syndrome

Keyword(s):  
2021 ◽  
Vol 132 (2) ◽  
pp. S42-S43
Author(s):  
Bernhard Gentner ◽  
Maria Ester Bernardo ◽  
Francesca Tucci ◽  
Francesca Fumagalli ◽  
Silvia Pontesilli ◽  
...  

2021 ◽  
Vol 385 (21) ◽  
pp. 1929-1940 ◽  
Author(s):  
Bernhard Gentner ◽  
Francesca Tucci ◽  
Stefania Galimberti ◽  
Francesca Fumagalli ◽  
Maurizio De Pellegrin ◽  
...  

2001 ◽  
Vol 120 (5) ◽  
pp. A349-A349
Author(s):  
J TSENG ◽  
F FARNEBO ◽  
O KISKER ◽  
C BECKER ◽  
C KUO ◽  
...  

2005 ◽  
Vol 173 (4S) ◽  
pp. 300-300
Author(s):  
Sreedhar Sagi ◽  
Lutz Trojan ◽  
Peter Aiken ◽  
Maurice S. Michel ◽  
Thomas Knoll

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