scholarly journals A Phase I/IIa Safety and Efficacy Study of Nebulized Liposome-mediated Gene Therapy for Cystic Fibrosis Supports a Multidose Trial

2015 ◽  
Vol 192 (11) ◽  
pp. 1389-1392 ◽  
Author(s):  
Eric W. F. W. Alton ◽  
A. Christopher Boyd ◽  
David J. Porteous ◽  
Gwyneth Davies ◽  
Jane C. Davies ◽  
...  
Keyword(s):  
Cystic Fibrosis ◽  
Gene Therapy ◽  
Phase I ◽  
Efficacy Study ◽  
Safety And Efficacy

scholarly journals AAV-Mediated Gene Therapy for Galactosialidosis: A Long-term Safety and Efficacy Study

2021 ◽  
Author(s):  
Huimin Hu ◽  
Rosario Mosca ◽  
Elida Gomero ◽  
Diantha van de Vlekkert ◽  
Yvan Campos ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Efficacy Study ◽  
Safety And Efficacy

Gene Therapy for Cystic Fibrosis Using E1-Deleted Adenovirus: A Phase I Trial in the Nasal Cavity. University of North Carolina at Chapel Hill, Chapel Hill, North Carolina

1994 ◽  
Vol 5 (5) ◽  
pp. 615-639 ◽  
Author(s):  
Richard C. Boucher ◽  
Michael R. Knowles ◽  
Larry G. Johnson ◽  
John C. Olsen ◽  
Raymond Pickles ◽  
...  
Keyword(s):  
Cystic Fibrosis ◽  
Gene Therapy ◽  
North Carolina ◽  
Phase I ◽  
Nasal Cavity ◽  
Phase I Trial ◽  
University Of North Carolina ◽  
Chapel Hill
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