ScienceGate
Advanced Search
Author Search
Journal Finder
Blog
Sign in / Sign up
ScienceGate
Search
Author Search
Journal Finder
Blog
Sign in / Sign up
Gene therapy for X-linked severe combined immunodeficiency and other hereditary diseases
Gene Therapy: Technologies & Applications
◽
10.2217/ebo.12.156
◽
2013
◽
pp. 58-69
Author(s):
Salima Hacein-Bey-Abina
◽
Alain Fischer
◽
Marina Cavazzana-Calvo
Keyword(s):
Gene Therapy
◽
Severe Combined Immunodeficiency
◽
Hereditary Diseases
◽
Combined Immunodeficiency
Download Full-text
Related Documents
Cited By
References
Faculty Opinions recommendation of Sustained correction of X-linked severe combined immunodeficiency by ex vivo gene therapy.
Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature
◽
10.3410/f.1005837.70356
◽
2002
◽
Author(s):
Seppo Yla-Herttuala
Keyword(s):
Gene Therapy
◽
Ex Vivo
◽
Severe Combined Immunodeficiency
◽
Combined Immunodeficiency
◽
Ex Vivo Gene Therapy
Download Full-text
Faculty Opinions recommendation of Long-term persistence of a polyclonal T cell repertoire after gene therapy for X-linked severe combined immunodeficiency.
Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature
◽
10.3410/f.13489119.14866267
◽
2012
◽
Author(s):
Nichola Cooper
◽
Ilaria Terrinoni
Keyword(s):
Gene Therapy
◽
T Cell
◽
Severe Combined Immunodeficiency
◽
T Cell Repertoire
◽
Combined Immunodeficiency
◽
Cell Repertoire
Download Full-text
Faculty Opinions recommendation of Correction of murine Rag2 severe combined immunodeficiency by lentiviral gene therapy using a codon-optimized RAG2 therapeutic transgene.
Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature
◽
10.3410/f.722644269.793515036
◽
2016
◽
Author(s):
Fabio Candotti
Keyword(s):
Gene Therapy
◽
Severe Combined Immunodeficiency
◽
Combined Immunodeficiency
◽
Lentiviral Gene Therapy
Download Full-text
Faculty Opinions recommendation of Hematopoietic stem cell gene therapy for adenosine deaminase-deficient severe combined immunodeficiency leads to long-term immunological recovery and metabolic correction.
Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature
◽
10.3410/f.720388464.793515025
◽
2016
◽
Author(s):
Fabio Candotti
Keyword(s):
Gene Therapy
◽
Severe Combined Immunodeficiency
◽
Combined Immunodeficiency
◽
Hematopoietic Stem
◽
Immunological Recovery
◽
Metabolic Correction
◽
Cell Gene
◽
Stem Cell Gene
◽
Stem Cell Gene Therapy
Download Full-text
B-cell function in severe combined immunodeficiency after stem cell or gene therapy: A review
Journal of Allergy and Clinical Immunology
◽
10.1016/j.jaci.2010.02.012
◽
2010
◽
Vol 125
(4)
◽
pp. 790-797
◽
Cited By ~ 39
Author(s):
Rebecca H. Buckley
Keyword(s):
Gene Therapy
◽
Stem Cell
◽
B Cell
◽
Cell Function
◽
Severe Combined Immunodeficiency
◽
Combined Immunodeficiency
◽
B Cell Function
◽
Or Gene
Download Full-text
Preclinical Development of a Lentiviral Vector for Gene Therapy of X-Linked Severe Combined Immunodeficiency
Molecular Therapy — Methods & Clinical Development
◽
10.1016/j.omtm.2018.03.002
◽
2018
◽
Vol 9
◽
pp. 257-269
◽
Cited By ~ 17
Author(s):
Valentina Poletti
◽
Sabine Charrier
◽
Guillaume Corre
◽
Bernard Gjata
◽
Alban Vignaud
◽
...
Keyword(s):
Gene Therapy
◽
Lentiviral Vector
◽
Severe Combined Immunodeficiency
◽
Combined Immunodeficiency
◽
Preclinical Development
Download Full-text
Successful Gene Therapy for Severe Combined Immunodeficiency
New England Journal of Medicine
◽
10.1056/nejm200204183461612
◽
2002
◽
Vol 346
(16)
◽
pp. 1241-1243
◽
Cited By ~ 7
Author(s):
Fred S. Rosen
Keyword(s):
Gene Therapy
◽
Severe Combined Immunodeficiency
◽
Combined Immunodeficiency
Download Full-text
T cell dynamics and response of the microbiota after gene therapy to treat X-linked severe combined immunodeficiency
Genome Medicine
◽
10.1186/s13073-018-0580-z
◽
2018
◽
Vol 10
(1)
◽
Cited By ~ 12
Author(s):
Erik L. Clarke
◽
A. Jesse Connell
◽
Emmanuelle Six
◽
Nadia A. Kadry
◽
Arwa A. Abbas
◽
...
Keyword(s):
Gene Therapy
◽
T Cell
◽
Severe Combined Immunodeficiency
◽
Combined Immunodeficiency
◽
Cell Dynamics
Download Full-text
Gene Therapy of X-Linked Severe Combined Immunodeficiency
Cytokines and Colony Stimulating Factors
◽
10.1385/1-59259-345-3:247
◽
2003
◽
pp. 247-260
Author(s):
Salima Hacein-Bey-Abina
◽
Genevieve de Saint Basile
◽
Marina Cavazzana-Calvo
Keyword(s):
Gene Therapy
◽
Severe Combined Immunodeficiency
◽
Combined Immunodeficiency
Download Full-text
Gene Therapy Clinical Trials for Adenosine Deaminase Deficiency/Severe Combined Immunodeficiency
Clinical Trials of Genetic Therapy with Antisense DNA and DNA Vectors
◽
10.4324/9781003064657-6
◽
2020
◽
pp. 111-131
Author(s):
Eriinda M. Gordon
◽
W. French Anderson
Keyword(s):
Gene Therapy
◽
Clinical Trials
◽
Adenosine Deaminase
◽
Severe Combined Immunodeficiency
◽
Combined Immunodeficiency
◽
Adenosine Deaminase Deficiency
Download Full-text
Sign in / Sign up
Close
Export Citation Format
Close
Share Document
Close