Gene therapy for X-linked severe combined immunodeficiency and other hereditary diseases

Author(s):  
Salima Hacein-Bey-Abina ◽  
Alain Fischer ◽  
Marina Cavazzana-Calvo
2018 ◽  
Vol 9 ◽  
pp. 257-269 ◽  
Author(s):  
Valentina Poletti ◽  
Sabine Charrier ◽  
Guillaume Corre ◽  
Bernard Gjata ◽  
Alban Vignaud ◽  
...  

2018 ◽  
Vol 10 (1) ◽  
Author(s):  
Erik L. Clarke ◽  
A. Jesse Connell ◽  
Emmanuelle Six ◽  
Nadia A. Kadry ◽  
Arwa A. Abbas ◽  
...  

Author(s):  
Salima Hacein-Bey-Abina ◽  
Genevieve de Saint Basile ◽  
Marina Cavazzana-Calvo

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