Orphan designation: Adeno-associated viral vector serotype 2/6 encoding zinc-finger nucleases and the human iduronate 2-sulfatase gene, Treatment of mucopolysaccharidosis type II (Hunter's syndrome)

Case Medical Research ◽

10.31525/cmr-18ec39f ◽

2019 ◽

Author(s):

Keyword(s):

Zinc Finger ◽

Viral Vector ◽

Zinc Finger Nucleases ◽

Mucopolysaccharidosis Type ◽

Type Ii ◽

Mucopolysaccharidosis Type Ii ◽

Orphan Designation ◽

Gene Treatment ◽

Hunter's Syndrome

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Orphan designation: Adeno-associated viral vector serotype 2/6 encoding zinc-finger nucleases and the human alpha L-iduronidase gene, Treatment of mucopolysaccharidosis type I

Case Medical Research ◽

10.31525/cmr-18ec3a4 ◽

2019 ◽

Author(s):

Keyword(s):

Zinc Finger ◽

Viral Vector ◽

Zinc Finger Nucleases ◽

Type I ◽

Mucopolysaccharidosis Type ◽

Mucopolysaccharidosis Type I ◽

Orphan Designation ◽

Gene Treatment

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Orphan designation: Humanised IGg1 monoclonal antibody targeting human transferrin receptor conjugated to human iduronate-2-sulfatase, Treatment of mucopolysaccharidosis type II (Hunter’s syndrome)

Case Medical Research ◽

10.31525/cmr-fb98ae ◽

2019 ◽

Author(s):

Keyword(s):

Monoclonal Antibody ◽

Transferrin Receptor ◽

Mucopolysaccharidosis Type ◽

Type Ii ◽

Mucopolysaccharidosis Type Ii ◽

Orphan Designation ◽

Human Transferrin ◽

Human Transferrin Receptor ◽

Igg1 Monoclonal Antibody ◽

Hunter's Syndrome

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Orphan designation: Humanised IGg1 monoclonal antibody targeting human transferrin receptor conjugated to human iduronate-2-sulfatase, Treatment of mucopolysaccharidosis type II (Hunter’s syndrome)

Case Medical Research ◽

10.31525/cmr-fb7ce7 ◽

2019 ◽

Author(s):

Keyword(s):

Monoclonal Antibody ◽

Transferrin Receptor ◽

Mucopolysaccharidosis Type ◽

Type Ii ◽

Mucopolysaccharidosis Type Ii ◽

Orphan Designation ◽

Human Transferrin ◽

Human Transferrin Receptor ◽

Igg1 Monoclonal Antibody ◽

Hunter's Syndrome

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TREATMENT OPTIONS FOR MUCOPOLYSACCHARIDOSIS TYPE II (HUNTER'S SYNDROME)

Enzyme Technologies ◽

10.1002/9781118739907.ch8 ◽

2013 ◽

pp. 301-319

Author(s):

Michael Beck

Keyword(s):

Treatment Options ◽

Mucopolysaccharidosis Type ◽

Type Ii ◽

Mucopolysaccharidosis Type Ii ◽

Hunter's Syndrome

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Tracheostomy in mucopolysaccharidosis type II (Hunter's Syndrome)

International Journal of Pediatric Otorhinolaryngology ◽

10.1016/j.ijporl.2013.05.002 ◽

2013 ◽

Vol 77 (7) ◽

pp. 1204-1208 ◽

Cited By ~ 10

Author(s):

Vikas Malik ◽

Jaya Nichani ◽

Michael P. Rothera ◽

James Edmond Wraith ◽

Simon A. Jones ◽

...

Keyword(s):

Mucopolysaccharidosis Type ◽

Type Ii ◽

Mucopolysaccharidosis Type Ii ◽

Hunter's Syndrome

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Severe aortic stenosis in systemic lupus erythematosus and mucopolysaccharidosis type II (hunter's syndrome)

Clinical Cardiology ◽

10.1002/clc.4960111014 ◽

1988 ◽

Vol 11 (10) ◽

pp. 723-725 ◽

Cited By ~ 5

Author(s):

B. Zimmermann ◽

E. V. Lally ◽

S. C. Sharma ◽

F. J. Schoen ◽

S. R. Kaplan

Keyword(s):

Systemic Lupus Erythematosus ◽

Aortic Stenosis ◽

Lupus Erythematosus ◽

Severe Aortic Stenosis ◽

Mucopolysaccharidosis Type ◽

Type Ii ◽

Mucopolysaccharidosis Type Ii ◽

Systemic Lupus ◽

Hunter's Syndrome

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Challenges in the Management of Mucopolysaccharidosis Type II (Hunter’s Syndrome) in a Developing Country: a Case Report

Ethiopian Journal of Health Sciences ◽

10.4314/ejhs.v25i3.12 ◽

2015 ◽

Vol 25 (3) ◽

pp. 279

Author(s):

R Ibraheem ◽

P Oladele ◽

A AbdulAzeez ◽

M Abdulkadri ◽

S Katibi ◽

...

Keyword(s):

Case Report ◽

Developing Country ◽

Mucopolysaccharidosis Type ◽

Type Ii ◽

Mucopolysaccharidosis Type Ii ◽

Hunter's Syndrome

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Retroviral transduction and expansion of peripheral blood lymphocytes for the treatment of mucopolysaccharidosis type II, Hunter's syndrome

Transfusion ◽

10.1046/j.1537-2995.1999.39499235664.x ◽

1999 ◽

Vol 39 (4) ◽

pp. 343-350 ◽

Cited By ~ 16

Author(s):

David F. Stroncek ◽

Allison Hubel ◽

Raji A. Shankar ◽

Scott R. Burger ◽

Dao Pan ◽

...

Keyword(s):

Peripheral Blood ◽

Peripheral Blood Lymphocytes ◽

Mucopolysaccharidosis Type ◽

Type Ii ◽

Mucopolysaccharidosis Type Ii ◽

Retroviral Transduction ◽

Blood Lymphocytes ◽

Hunter's Syndrome

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Mucopolysaccharidosis type II (Hunter's syndrome) – A clinical case report

Journal of Indian College of Cardiology ◽

10.1016/j.jicc.2014.07.004 ◽

2015 ◽

Vol 5 (1) ◽

pp. 61-66 ◽

Cited By ~ 1

Author(s):

Rajeev Gupta ◽

Chandra Bhushan Pandey ◽

Sunil Tripathi

Keyword(s):

Case Report ◽

Clinical Case ◽

Mucopolysaccharidosis Type ◽

Type Ii ◽

Mucopolysaccharidosis Type Ii ◽

Hunter's Syndrome

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Failure of the laryngeal mask to secure the airway in a patient with Hunter's syndrome (mucopolysaccharidosis type II)

Pediatric Anesthesia ◽

10.1046/j.1460-9592.1999.9220289.x ◽

1999 ◽

Vol 9 (2) ◽

pp. 153-155 ◽

Cited By ~ 13

Author(s):

PAOLO BUSONI ◽

GIULIANA FOGNANI

Keyword(s):

Laryngeal Mask ◽

Mucopolysaccharidosis Type ◽

Type Ii ◽

Mucopolysaccharidosis Type Ii ◽

Hunter's Syndrome

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