Faculty Opinions recommendation of An ex vivo gene therapy approach to treat muscular dystrophy using inducible pluripotent stem cells.

Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature ◽

10.3410/f.717987156.793477222 ◽

2013 ◽

Author(s):

Denis Guttridge

Keyword(s):

Stem Cells ◽

Gene Therapy ◽

Muscular Dystrophy ◽

Pluripotent Stem Cells ◽

Ex Vivo ◽

Therapy Approach ◽

Gene Therapy Approach ◽

Ex Vivo Gene Therapy

Download Full-text

An ex vivo gene therapy approach to treat muscular dystrophy using inducible pluripotent stem cells

Nature Communications ◽

10.1038/ncomms2550 ◽

2013 ◽

Vol 4 (1) ◽

Cited By ~ 91

Author(s):

Antonio Filareto ◽

Sarah Parker ◽

Radbod Darabi ◽

Luciene Borges ◽

Michelina Iacovino ◽

...

Keyword(s):

Stem Cells ◽

Gene Therapy ◽

Muscular Dystrophy ◽

Pluripotent Stem Cells ◽

Ex Vivo ◽

Therapy Approach ◽

Gene Therapy Approach ◽

Ex Vivo Gene Therapy

Download Full-text

Autologous cell/gene therapy approach of hemophilia B using patient specific induced Pluripotent Stem Cells

Journal of Hepatology ◽

10.1016/s0168-8278(18)30381-7 ◽

2018 ◽

Vol 68 ◽

pp. S81-S82

Author(s):

E. Luce ◽

C. Steichen ◽

M. Antonietta ◽

S. Goulinet ◽

T. Lambert ◽

...

Keyword(s):

Stem Cells ◽

Gene Therapy ◽

Induced Pluripotent Stem Cells ◽

Pluripotent Stem Cells ◽

Patient Specific ◽

Therapy Approach ◽

Gene Therapy Approach ◽

Autologous Cell ◽

Induced Pluripotent ◽

Cell Gene

Download Full-text

Ex-Vivo Gene Therapy Approach for Continuous Delivery of BDNF and Its Potential Use for Neurological Disorders (P02.013)

Neurology ◽

10.1212/wnl.78.1_meetingabstracts.p02.013 ◽

2012 ◽

Vol 78 (Meeting Abstracts 1) ◽

pp. P02.013-P02.013

Author(s):

A. Gomez-Vargas ◽

G. Hortelano ◽

M. Rathbone

Keyword(s):

Gene Therapy ◽

Neurological Disorders ◽

Ex Vivo ◽

Therapy Approach ◽

Gene Therapy Approach ◽

Continuous Delivery ◽

Ex Vivo Gene Therapy ◽

Potential Use

Download Full-text

1093. Ex Vivo Gene Therapy Approach Using Human Lim Mineralization Protein_3 To Induce Bone Healing in a Rodent Model

Molecular Therapy ◽

10.1016/j.ymthe.2006.08.1196 ◽

2006 ◽

Vol 13 ◽

pp. S420

Author(s):

Enrico Pola ◽

Wanda Lattanzi ◽

Giandomenico Logroscino ◽

Giovanni Pecorini ◽

Anna Tampieri ◽

...

Keyword(s):

Gene Therapy ◽

Bone Healing ◽

Ex Vivo ◽

Rodent Model ◽

Therapy Approach ◽

Gene Therapy Approach ◽

Ex Vivo Gene Therapy

Download Full-text

222. Lentiviral Vector-Based Ex Vivo Gene Therapy Approach for Metachromatic (MLD) and Globoid (GLD) Leukodystrophies

Molecular Therapy ◽

10.1016/s1525-0016(16)40664-7 ◽

2003 ◽

Vol 7 (5) ◽

pp. S88

Keyword(s):

Gene Therapy ◽

Lentiviral Vector ◽

Ex Vivo ◽

Therapy Approach ◽

Gene Therapy Approach ◽

Ex Vivo Gene Therapy

Download Full-text

Ex-Vivo Gene Therapy Approach for Continuous Delivery of BDNF and Its Potential Use for Neurological Disorders (IN6-1.008)

Neurology ◽

10.1212/wnl.78.1_meetingabstracts.in6-1.008 ◽

2012 ◽

Vol 78 (Meeting Abstracts 1) ◽

pp. IN6-1.008-IN6-1.008

Author(s):

A. Gomez-Vargas ◽

G. Hortelano ◽

M. Rathbone

Keyword(s):

Gene Therapy ◽

Neurological Disorders ◽

Ex Vivo ◽

Therapy Approach ◽

Gene Therapy Approach ◽

Continuous Delivery ◽

Ex Vivo Gene Therapy ◽

Potential Use

Download Full-text

Adult rat liver cells transdifferentiated with lentiviral IPF1 vectors reverse diabetes in mice: an ex vivo gene therapy approach

Diabetologia ◽

10.1007/s00125-006-0509-8 ◽

2006 ◽

Vol 50 (1) ◽

pp. 121-130 ◽

Cited By ~ 29

Author(s):

A. Fodor ◽

C. Harel ◽

L. Fodor ◽

M. Armoni ◽

P. Salmon ◽

...

Keyword(s):

Gene Therapy ◽

Rat Liver ◽

Ex Vivo ◽

Liver Cells ◽

Therapy Approach ◽

Gene Therapy Approach ◽

Adult Rat ◽

Diabetes In Mice ◽

Rat Liver Cells ◽

Ex Vivo Gene Therapy

Download Full-text

865. An Ex Vivo Gene Therapy Approach for Metachromatic Leukodystrophy Using Neural Progenitor Cells

Molecular Therapy ◽

10.1016/j.ymthe.2004.06.772 ◽

2004 ◽

Vol 9 ◽

pp. S329

Keyword(s):

Gene Therapy ◽

Progenitor Cells ◽

Neural Progenitor Cells ◽

Metachromatic Leukodystrophy ◽

Ex Vivo ◽

Neural Progenitor ◽

Therapy Approach ◽

Gene Therapy Approach ◽

Ex Vivo Gene Therapy

Download Full-text

Generation of induced pluripotent stem cells-derived hepatocyte-like cells for ex vivo gene therapy of primary hyperoxaluria type 1

Stem Cell Research ◽

10.1016/j.scr.2019.101467 ◽

2019 ◽

Vol 38 ◽

pp. 101467 ◽

Cited By ~ 7

Author(s):

Julie Estève ◽

Jean-Marc Blouin ◽

Magalie Lalanne ◽

Lamia Azzi-Martin ◽

Pierre Dubus ◽

...

Keyword(s):

Stem Cells ◽

Gene Therapy ◽

Pluripotent Stem Cells ◽

Ex Vivo ◽

Primary Hyperoxaluria ◽

Primary Hyperoxaluria Type 1 ◽

Ex Vivo Gene Therapy ◽

Induced Pluripotent ◽

Hyperoxaluria Type

Download Full-text

183. Development of Ex-Vivo Gene Therapy Procedures for Central Nervous System Diseases, Based on Homologous Recombination in Human Neural Stem Cells

Molecular Therapy ◽

10.1016/j.ymthe.2005.06.186 ◽

2005 ◽

Vol 11 ◽

pp. S71-S72

Keyword(s):

Stem Cells ◽

Gene Therapy ◽

Central Nervous System ◽

Nervous System ◽

Homologous Recombination ◽

Ex Vivo ◽

Nervous System Diseases ◽

Central Nervous System Diseases ◽

Human Neural Stem Cells ◽

Ex Vivo Gene Therapy

Download Full-text