Astellas Discloses Death of Fourth Boy Enrolled in its Gene Therapy Trial

Clinical OMICs ◽

10.1089/clinomi.08.06.06 ◽

2021 ◽

Vol 8 (6) ◽

pp. 5-5

Keyword(s):

Gene Therapy ◽

Gene Therapy Trial ◽

Its Gene ◽

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Design, Baseline Characteristics, and 2-Year Follow-up from The MPS IIIA Natural History Study Used as Control Group in Gene Therapy Trial

10.1055/s-0039-1685419 ◽

2019 ◽

Author(s):

B. Heron ◽

A. Chakrapani ◽

P. Drevot ◽

R. Giugliani ◽

N. Muschol ◽

...

Keyword(s):

Gene Therapy ◽

Natural History ◽

Control Group ◽

Natural History Study ◽

Gene Therapy Trial ◽

Baseline Characteristics ◽

Therapy Trial ◽

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Faculty Opinions recommendation of Long-term follow-up of a randomized AAV2-GAD gene therapy trial for Parkinson's disease.

Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature ◽

10.3410/f.727492597.793530605 ◽

2017 ◽

Author(s):

Laurent Villard

Keyword(s):

Parkinson’S Disease ◽

Gene Therapy ◽

Parkinson's Disease ◽

Gene Therapy Trial ◽

Long Term Follow Up ◽

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Development of a Gene Therapy Trial for Metastatic Prostate Cancer

10.21236/ada473358 ◽

2006 ◽

Author(s):

Thomas A. Gardner

Keyword(s):

Prostate Cancer ◽

Gene Therapy ◽

Metastatic Prostate Cancer ◽

Gene Therapy Trial ◽

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Development of a Gene Therapy Trial for Metastatic Prostate Cancer

10.21236/ada494544 ◽

2008 ◽

Author(s):

Thomas A. Gardner

Keyword(s):

Prostate Cancer ◽

Gene Therapy ◽

Metastatic Prostate Cancer ◽

Gene Therapy Trial ◽

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ASPIRO Gene Therapy Trial in X-Linked Myotubular Myopathy (XLMTM): Update on Preliminary Efficacy and Safety Findings

10.1055/s-0041-1739645 ◽

2021 ◽

Author(s):

A. Blaschek ◽

P. B. Shieh ◽

N. Kuntz ◽

J. J. Dowling ◽

W. Müller-Felber ◽

...

Keyword(s):

Gene Therapy ◽

Efficacy And Safety ◽

Myotubular Myopathy ◽

Gene Therapy Trial ◽

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Gene therapy for breast cancer. — review of clinical gene therapy trials for breast cancer and mdr1 gene therapy trial in cancer institute hospital

Breast Cancer ◽

10.2325/jbcs.13.8 ◽

2006 ◽

Vol 13 (1) ◽

pp. 8-15 ◽

Author(s):

Shunji Takahashi ◽

Yoshinori Ito ◽

Kiyohiko Hatake ◽

Yoshikazu Sugimoto

Keyword(s):

Breast Cancer ◽

Gene Therapy ◽

Mdr1 Gene ◽

Cancer Institute Hospital ◽

Gene Therapy Trial ◽

Institute Hospital ◽

Cancer Review ◽

Clinical Gene Therapy ◽

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Steps in a Translational Cancer Gene Therapy Trial

Cancer Drug Discovery and Development - Gene Therapy for Cancer ◽

10.1007/978-1-59745-222-9_25 ◽

2007 ◽

pp. 447-460

Author(s):

Urs W. von Holzen ◽

Stephen G. Swisher

Keyword(s):

Gene Therapy ◽

Cancer Gene Therapy ◽

Cancer Gene ◽

Gene Therapy Trial ◽

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Popping the Bubble: Promising Results From a Phase I-II Lentiviral Gene Therapy Trial for X-SCID

The Hematologist ◽

10.1182/hem.v16.4.9661 ◽

2019 ◽

Vol 16 (4) ◽

Author(s):

David T. Teachey ◽

Danielle E. Arnold

Keyword(s):

Gene Therapy ◽

Phase I ◽

Gene Therapy Trial ◽

Therapy Trial ◽

Lentiviral Gene Therapy

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NIH Recombinant DNA Advisory Committee Continues to Ponder Adverse Event Associated With AAV Gene Therapy Trial

Molecular Therapy ◽

10.1038/mt.2008.2 ◽

2008 ◽

Vol 16 (3) ◽

pp. 427-428 ◽

Author(s):

David A Williams

Keyword(s):

Gene Therapy ◽

Adverse Event ◽

Advisory Committee ◽

Recombinant Dna ◽

Gene Therapy Trial ◽

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Single-dose AAV9-CLN6 gene transfer stabilizes motor and language function in CLN6-type Batten disease: Interim results from the first clinical gene therapy trial

Molecular Genetics and Metabolism ◽

10.1016/j.ymgme.2019.11.101 ◽

2020 ◽

Vol 129 (2) ◽

pp. S46-S47

Author(s):

Emily de los Reyes ◽

Kathrin Meyer ◽

Lenora Lehwald ◽

Charles Albright ◽

Jeff Castelli ◽

...

Keyword(s):

Gene Therapy ◽

Single Dose ◽

Gene Transfer ◽

Batten Disease ◽

Language Function ◽

Gene Therapy Trial ◽

Clinical Gene Therapy ◽

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