scholarly journals AAV-Mediated Gene Therapy in the Guanylate Cyclase (RetGC1/RetGC2) Double Knockout Mouse Model of Leber Congenital Amaurosis

2013 ◽  
Vol 24 (2) ◽  
pp. 189-202 ◽  
Author(s):  
Sanford L. Boye ◽  
Igor V. Peshenko ◽  
Wei Chieh Huang ◽  
Seok Hong Min ◽  
Issam McDoom ◽  
...  
2016 ◽  
Vol 214 (1) ◽  
pp. S135
Author(s):  
Hind N. Moussa ◽  
Baha M. Sibai ◽  
Sean C. Blackwell ◽  
David A. Fournie ◽  
Alejandra E. Ontiveros ◽  
...  

2010 ◽  
Vol 12 (Suppl 1) ◽  
pp. P1 ◽  
Author(s):  
Jon O Cleary ◽  
Karen McCue ◽  
Anthony N Price ◽  
Sarah Beddow ◽  
Roger J Ordidge ◽  
...  

Gene Therapy ◽  
2015 ◽  
Vol 22 (8) ◽  
pp. 619-627 ◽  
Author(s):  
H Zhong ◽  
A Eblimit ◽  
Y Moayedi ◽  
S L Boye ◽  
V A Chiodo ◽  
...  

Hepatology ◽  
2019 ◽  
Author(s):  
Daniel Rizzolo ◽  
Kyle Buckley ◽  
Bo Kong ◽  
Le Zhan ◽  
Jianliang Shen ◽  
...  

2015 ◽  
Vol 29 (S1) ◽  
Author(s):  
Emilia Boiadjieva ◽  
Clara Vilches ◽  
Susanna Bodoy ◽  
Lalita Oparija ◽  
Julia Jando ◽  
...  

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