Gene Replacement Therapy Rescues Photoreceptor Degeneration in a Murine Model of Leber Congenital Amaurosis Lacking RPGRIP

2005 ◽  
Vol 46 (9) ◽  
pp. 3039 ◽  
Author(s):  
Basil S. Pawlyk ◽  
Alexander J. Smith ◽  
Prateek K. Buch ◽  
Michael Adamian ◽  
Dong-Hyun Hong ◽  
...  
Keyword(s):  
Replacement Therapy ◽  
Murine Model ◽  
Gene Replacement ◽  
Photoreceptor Degeneration ◽  
Leber Congenital Amaurosis ◽  
Gene Replacement Therapy

scholarly journals Long-term rescue of cone photoreceptor degeneration in retinitis pigmentosa 2 (RP2)-knockout mice by gene replacement therapy

2015 ◽  
Vol 24 (22) ◽  
pp. 6446-6458 ◽  
Author(s):  
Suddhasil Mookherjee ◽  
Suja Hiriyanna ◽  
Kayleigh Kaneshiro ◽  
Linjing Li ◽  
Yichao Li ◽  
...  
Keyword(s):  
Retinitis Pigmentosa ◽  
Replacement Therapy ◽  
Knockout Mice ◽  
Gene Replacement ◽  
Cone Photoreceptor ◽  
Photoreceptor Degeneration ◽  
Gene Replacement Therapy

scholarly journals MEN1 Gene Replacement Therapy Reduces Proliferation Rates in a Mouse Model of Pituitary Adenomas

2012 ◽  
Vol 72 (19) ◽  
pp. 5060-5068 ◽  
Author(s):  
Gerard V. Walls ◽  
Manuel C. Lemos ◽  
Mahsa Javid ◽  
Miriam Bazan-Peregrino ◽  
Jeshmi Jeyabalan ◽  
...  
Keyword(s):  
Mouse Model ◽  
Replacement Therapy ◽  
Pituitary Adenomas ◽  
Gene Replacement ◽  
Men1 Gene ◽  
Gene Replacement Therapy

Delivery of cytosolic liver arginase into the mitochondrial matrix space: A possible novel site for gene replacement therapy

1996 ◽  
Vol 22 (6) ◽  
pp. 489-498 ◽  
Author(s):  
Paul B. Wissmann ◽  
Barbara K. Goodman ◽  
Joseph G. Vockley ◽  
Rita M. Kern ◽  
Stephen D. Cederbaum ◽  
...  
Keyword(s):  
Replacement Therapy ◽  
Gene Replacement ◽  
Mitochondrial Matrix ◽  
Matrix Space ◽  
Gene Replacement Therapy

scholarly journals Replacement Gene Therapy with a HumanRPGRIP1Sequence Slows Photoreceptor Degeneration in a Murine Model of Leber Congenital Amaurosis

2010 ◽  
Vol 21 (8) ◽  
pp. 993-1004 ◽  
Author(s):  
Basil S. Pawlyk ◽  
Oleg V. Bulgakov ◽  
Xiaoqing Liu ◽  
Xiaoyun Xu ◽  
Michael Adamian ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Murine Model ◽  
Photoreceptor Degeneration ◽  
Leber Congenital Amaurosis
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