Intravitreal administration of small molecule read-through agents demonstrate functional activity in a nonsense mutation mouse model
2020 ◽
Vol 201
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pp. 108274
Daniel K. Crawford
◽
Phillip Vanlandingham
◽
Susan Schneider
◽
Matthew M. Goddeeris
2007 ◽
Vol 104
(39)
◽
pp. 15394-15399
◽
C. Yang
◽
J. Feng
◽
W. Song
◽
J. Wang
◽
B. Tsai
◽
...
2016 ◽
Vol 12
(6)
◽
pp. 444-451
◽
Kumar N Alagramam
◽
Suhasini R Gopal
◽
Ruishuang Geng
◽
Daniel H-C Chen
◽
Ina Nemet
◽
...
2012 ◽
Vol 7
(3)
◽
pp. e33976
◽
Robin M. Hallett
◽
Maria K. Kondratyev
◽
Andrew O. Giacomelli
◽
Allison M. L. Nixon
◽
Adele Girgis-Gabardo
◽
...
2021 ◽
Vol 910
◽
pp. 174496
Keita Shibata
◽
Terumasa Hashimoto
◽
Keiji Hasumi
◽
Koji Nobe
Luqia Hou
◽
Guang Yang
◽
Shibing Tang
◽
Cynthia Alcazar
◽
Prajakta Joshi
◽
...
Jesus Campagna
◽
Patricia Spilman
◽
Barbara Jagodzinska
◽
Dongsheng Bai
◽
Asa Hatami
◽
...
2013 ◽
Vol 22
(12)
◽
pp. 2462-2470
◽
M. Jiang
◽
Q. Peng
◽
X. Liu
◽
J. Jin
◽
Z. Hou
◽
...
2019 ◽
Vol 235
(2)
◽
pp. 1259-1273
◽
Lele Li
◽
Manhui Zhu
◽
Wenli Wu
◽
Bai Qin
◽
Jiayi Gu
◽
...
2019 ◽
Vol 26
(3)
◽
pp. 1243-1249
◽
Brian M. Anderson
◽
Zall Hirschstein
◽
Zachary M. Novakovic
◽
Patricia Grasso