scholarly journals Efficacy of the pharmacologic chaperone migalastat in a subset of male patients with the classic phenotype of Fabry disease and migalastat-amenable variants: data from the phase 3 randomized, multicenter, double-blind clinical trial and extension study

2019 ◽  
Vol 21 (9) ◽  
pp. 1987-1997 ◽  
Author(s):  
Dominique P. Germain ◽  
Kathy Nicholls ◽  
Roberto Giugliani ◽  
Daniel G. Bichet ◽  
Derralynn A. Hughes ◽  
...  
Cancer ◽  
2010 ◽  
Vol 116 (14) ◽  
pp. 3513-3520 ◽  
Author(s):  
Pascal Jean-Pierre ◽  
Gary R. Morrow ◽  
Joseph A. Roscoe ◽  
Charles Heckler ◽  
Supriya Mohile ◽  
...  

Diabetes Care ◽  
2021 ◽  
pp. dc202995
Author(s):  
Thomas R. Pieber ◽  
Ronnie Aronson ◽  
Ulrike Hövelmann ◽  
Julie Willard ◽  
Leona Plum-Mörschel ◽  
...  

Sign in / Sign up

Export Citation Format

Share Document