Correction of murine mucopolysaccharidosis type IIIA central nervous system pathology by intracerebroventricular lentiviral-mediated gene delivery

Type Iiia ◽

Correction of mucopolysaccharidosis type IIIA somatic and central nervous system pathology by lentiviral-mediated gene transfer

The Journal of Gene Medicine ◽

10.1002/jgm.1489 ◽

2010 ◽

Vol 12 (9) ◽

pp. 717-728 ◽

Cited By ~ 25

Author(s):

Chantelle McIntyre ◽

Sharon Byers ◽

Donald S. Anson

Keyword(s):

Central Nervous System ◽

Nervous System ◽

Gene Transfer ◽

Type Iiia ◽

Therapeutic correction of central nervous system pathology by intravenously administered chemically modified sulfamidase in a mouse model of mucopolysaccharidosis type IIIA

Molecular Genetics and Metabolism ◽

10.1016/j.ymgme.2017.12.136 ◽

2018 ◽

Vol 123 (2) ◽

pp. S57

Author(s):

Susanne Gustavsson

Keyword(s):

Central Nervous System ◽

Nervous System ◽

Mouse Model ◽

Chemically Modified ◽

Type Iiia ◽

Intranasal Adeno-Associated Virus Mediated Gene Delivery and Expression of Human Iduronidase in the Central Nervous System: A Noninvasive and Effective Approach for Prevention of Neurologic Disease in Mucopolysaccharidosis Type I

Human Gene Therapy ◽

10.1089/hum.2017.187 ◽

2017 ◽

Vol 28 (7) ◽

pp. 576-587 ◽

Cited By ~ 19

Author(s):

Lalitha R. Belur ◽

Alexa Temme ◽

Kelly M. Podetz-Pedersen ◽

Maureen Riedl ◽

Lucy Vulchanova ◽

...

Keyword(s):

Central Nervous System ◽

Nervous System ◽

Gene Delivery ◽

Type I ◽

Neurologic Disease ◽

Mucopolysaccharidosis Type I ◽

Adeno Associated Virus ◽

System A ◽

The Central Nervous System

Central nervous system pathology as a cause of legal termination of pregnancy

10.26226/morressier.5b4709896f4cb30010952052 ◽

2018 ◽

Author(s):

Jessica Camacho

Keyword(s):

Central Nervous System ◽

Nervous System ◽

Termination Of Pregnancy ◽

Central Nervous System Pathology

Gene Therapy With Modified Autologous Hematopoietic Stem Cells for Patients With Mucopolysaccharidosis Type IIIA

Case Medical Research ◽

10.31525/ct1-nct04201405 ◽

2019 ◽

Author(s):

Keyword(s):

Stem Cells ◽

Gene Therapy ◽

Hematopoietic Stem Cells ◽

Hematopoietic Stem ◽

Type Iiia ◽

Cardiac disease as the presenting feature of mucopolysaccharidosis type IIIA: A case report

Molecular Genetics and Metabolism Reports ◽

10.1016/j.ymgmr.2014.09.003 ◽

2014 ◽

Vol 1 ◽

pp. 422-424 ◽

Cited By ~ 5

Author(s):

Erlane Marques Ribeiro ◽

Ana Carolina Brusius-Facchin ◽

Sandra Leistner-Segal ◽

Carlos Antônio Bruno da Silva ◽

Ida Vanessa Schwartz

Keyword(s):

Case Report ◽

Cardiac Disease ◽

Type Iiia ◽

Stability of mRNA/Cationic Lipid Lipoplexes in Human and Rat Cerebrospinal Fluid: Methods and Evidence for Nonviral mRNA Gene Delivery to the Central Nervous System

Human Gene Therapy ◽

10.1089/10430340360535751 ◽

2003 ◽

Vol 14 (3) ◽

pp. 191-202 ◽

Cited By ~ 39

Author(s):

Dua M. Anderson ◽

Leon L. Hall ◽

Anitha R. Ayyalapu ◽

Van R. Irion ◽

Michael H. Nantz ◽

...

Keyword(s):

Central Nervous System ◽

Cerebrospinal Fluid ◽

Nervous System ◽

Gene Delivery ◽

Cationic Lipid ◽

Mrna Gene ◽

The Central Nervous System

18F-FDG PET/CT in HIV-related central nervous system pathology

European Journal of Nuclear Medicine and Molecular Imaging ◽

10.1007/s00259-013-2448-1 ◽

2013 ◽

Vol 40 (9) ◽

pp. 1420-1427 ◽

Cited By ~ 17

Author(s):

Scarlett Lewitschnig ◽

Keerti Gedela ◽

Martina Toby ◽

Ranjababu Kulasegaram ◽

Mark Nelson ◽

...

Keyword(s):

Central Nervous System ◽

Nervous System ◽

Fdg Pet ◽

Pet Ct ◽

18F Fdg ◽

Fdg Pet Ct

Danger: High Voltage—The Role of Voltage-Gated Calcium Channels in Central Nervous System Pathology

Cells ◽

10.3390/cells6040043 ◽

2017 ◽

Vol 6 (4) ◽

pp. 43 ◽

Cited By ~ 9

Author(s):

Andrea Schampel ◽

Stefanie Kuerten

Keyword(s):

Central Nervous System ◽

Nervous System ◽

Calcium Channels ◽

High Voltage ◽

Voltage Gated ◽

Voltage Gated Calcium Channels

Characterization of Sulfated Oligosaccharides in Mucopolysaccharidosis Type IIIA by Electrospray Ionization Mass Spectrometry

Analytical Chemistry ◽

10.1021/ac052083d ◽

2006 ◽

Vol 78 (13) ◽

pp. 4534-4542 ◽

Cited By ~ 28

Author(s):

Kerryn E. Mason ◽

Peter J. Meikle ◽

John J. Hopwood ◽

Maria Fuller

Keyword(s):

Mass Spectrometry ◽

Electrospray Ionization ◽

Electrospray Ionization Mass Spectrometry ◽

Ionization Mass Spectrometry ◽

Ionization Mass ◽

Sulfated Oligosaccharides ◽

Type Iiia ◽