CRISPR for Neuromuscular Disorders: Gene Editing and Beyond
Keyword(s):
This is a review describing advances in CRISPR/Cas-mediated therapies for neuromuscular disorders (NMDs). We explore both CRISPR-mediated editing and dead Cas approaches as potential therapeutic strategies for multiple NMDs. Last, therapeutic considerations, including delivery and off-target effects, are also discussed.
2018 ◽
pp. 25-27
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Keyword(s):
2019 ◽
Vol 15
(4)
◽
pp. 291-303
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Keyword(s):